NCT00273910

Brief Summary

This study will evaluate the immunization effects of a vaccine for patients who are at risk for recurrence of their skin cancer. That is, the risk of cancer is higher if melanoma has invaded deep into the skin or lymph nodes. Currently, the only therapy that the U.S. Food and Drug Administration (FDA) has approved for preventing recurrence of melanoma is alpha-interferon. But the research data are controversial. In this study, the vaccine to be used, called gp100, contains a piece of a protein called a peptide, which melanoma cancer cells produce. Patients 16 and older who have had confirmed melanoma surgically removed and whose tissue type is tested as being human leukocyte antigen serotype within HLA-A serotype group (HLA-A2), through a specific blood test, may be eligible for this study. Up to 132 participants will be enrolled. There will be a physical examination and collection of blood samples for tests, and making sure that x-rays and scans are current. Patients will be randomly assigned to four groups. Group 1 will receive the peptide with an adjuvant (assistant) oil-based liquid called Montanide ISA-51, as an injection in the thigh. Group 2 will receive gp100, Montanide, and a cream called imiquimod, which the FDA has approved for treating genital warts and herpes but that may help immune cells in the skin to recognize the vaccine. Imiquimod will be applied to the skin for 5 days. Group 3 will receive gp100 mixed in salt water given as several mini-doses under the skin of the thigh. Group 4 will also receive several mini-doses of gp100 mixed in saline, as well as imiquimod cream applied to the skin for 5 days. All patients will receive the gp100 every 3 weeks for 12 weeks. Every dose is a cycle, with four cycles considered a course of therapy. If the melanoma does not return or patients do not experience side effects from this therapy, then the courses of vaccine will repeated for up to 12 cycles of therapy (3 courses over 33 weeks). Side effects of the peptide vaccination include local swelling, swelling of local lymph nodes, bruising, and pain and redness at the injection sites. There may be chills or fever. Patients will be watched closely for such side effects. To study how the vaccine changes the action of cells in the immune system, patients' white blood cells (lymphocytes) will be obtained, involving a separate informed consent. The procedure, called leukaphersis, requires inserting a needle into the arm, to obtain blood going into a machine, which divides the blood into red cells, plasma (or the serum part), and lymphocytes. The lymphocytes are removed, and the plasma and red cells returned to the patient through a second needle in the other arm. Risks associated with the procedure include fainting, which can be prevented by patients' eating before coming to the lab, and bleeding and infection at the needle site. Patients will undergo leukapheresis will be done about four times: before receiving the vaccine, 3 weeks after the first four doses, and then after 8 cycles and 12 cycles. Patients assigned to the groups receiving imiquimod will be asked to record every time they apply that cream and describe any symptoms developed during the study. All patients will be watched closely for any sign that their melanoma has returned. Before and throughout the study, multiple blood tests will be conducted. The vaccine, Montanide, and imiquimod may increase patients' immune system in fighting off new tumors, but that is not known now. However, the study may provide information that will be useful in treating melanoma patients in the future.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
104

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2006

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2006

Completed
6 days until next milestone

First Submitted

Initial submission to the registry

January 7, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 9, 2006

Completed
4.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2010

Completed
2.3 years until next milestone

Results Posted

Study results publicly available

August 14, 2012

Completed
Last Updated

October 19, 2012

Status Verified

October 1, 2012

Enrollment Period

4.3 years

First QC Date

January 7, 2006

Results QC Date

March 30, 2012

Last Update Submit

October 17, 2012

Conditions

Keywords

Disease Free Survivalgp 100:209-217 (210m)Immunologic ResponseAdjuvant TherapyCutaneous MelanomaMelanoma

Outcome Measures

Primary Outcomes (1)

  • Immunologic Response Rate

    Comparison of six different preparations of the gp100:209-217 (210M) melanoma antigen peptide. The arm with the greater number of immunologic responses will be the one most likely to be selected for future study on the basis of immunization alone. Evidence of immunization consist of at least 10 Elispots/100,000 cells above background. An injection site reaction is not an immune response.

    48 months

Secondary Outcomes (1)

  • Number of Participants With Adverse Events

    48 months

Study Arms (6)

Adj-3 A2 gp209(2M) in IFA SQ (vortex)

EXPERIMENTAL

gp100:209-217(210M) peptide emulsified in MONTANIDE ISA-51 or Montanide ISA 51 VG injected subcutaneously on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks).

Drug: gp100:209-217 (210M)Drug: Montanide ISA-51

Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (vortex)

EXPERIMENTAL

gp100:209-217(210M) peptide emulsified in MONTANIDE ISA-51 or Montanide ISA 51 VG injected subcutaneously on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks); following the injection patients will apply imiquimod to the skin at the site of injection daily for 5 days.

Drug: gp100:209-217 (210M)Drug: Montanide ISA-51Drug: Imiquimod

Adj-3 A2 gp209(2M) in saline ID

EXPERIMENTAL

gp100:209-217(210M) in 0.9% Sodium Chloride Injection injected intradermally on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks).

Drug: gp100:209-217 (210M)

Adj-3 A2 gp209(2M) in saline ID + Imiquimod

EXPERIMENTAL

gp100:209-217(210M) peptide in 0.9% Sodium Chloride Injection injected intradermally on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks); following the injection patients will apply imiquimod to the skin at the site of the injection daily for 5 days.

Drug: gp100:209-217 (210M)Drug: Imiquimod

Adj-3 A2 gp209(2M) in IFA SQ (2 Syringe)

EXPERIMENTAL

gp100:209-217(210M) peptide emulsified in Montanide ISA 51 VG injected subcutaneously on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks).

Drug: gp100:209-217 (210M)Drug: Montanide ISA-51

Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (2 Syringe)

EXPERIMENTAL

gp100:209-217(210M) peptide emulsified in Montanide ISA 51 VG injected subcutaneously on day one every three weeks (1 cycle) for a total of twelve cycles (33 weeks); following the injection patients will apply imiquimod to the skin at the site of injection daily for 5 days.

Drug: gp100:209-217 (210M)Drug: Montanide ISA-51Drug: Imiquimod

Interventions

Adj-3 A2 gp209(2M) in IFA SQ (2 Syringe)Adj-3 A2 gp209(2M) in IFA SQ (vortex)Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (2 Syringe)Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (vortex)Adj-3 A2 gp209(2M) in saline IDAdj-3 A2 gp209(2M) in saline ID + Imiquimod
Adj-3 A2 gp209(2M) in IFA SQ (2 Syringe)Adj-3 A2 gp209(2M) in IFA SQ (vortex)Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (2 Syringe)Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (vortex)

Apply imiquimod 5% cream to the skin at the site of injection daily for 5 days

Also known as: Aldara
Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (2 Syringe)Adj-3 A2 gp209(2M) in IFA SQ + Imiquimod (vortex)Adj-3 A2 gp209(2M) in saline ID + Imiquimod

Eligibility Criteria

Age7 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • HLA-A 0201 patients, age greater than or equal to 16 years, primary melanomas with lesions that are ulcerated and greater than or equal to 2mm, or any lesions that are greater than or equal to 4.0 mm in thickness, or greater than or equal to1 positive lymph node, or local recurrence, or resected metastatic disease, within 6 months of surgical resection will be considered. Patients must be clinically disease free at the time of protocol entry as documented by radiologic studies within 6 weeks of patient entry.
  • Serum creatinine of 2.0 mg/dl or less
  • Total bilirubin 1.6 mg/dl or less, except for patients with Gilbert's Syndrome who must have a total bilirubin less than 3.0 mg/dl.
  • WBC 3000/mm\^3 or greater,
  • Platelet count 90,000 mm\^3 or greater,
  • Serum aspartate aminotransferase (AST)/alanine aminotransferase (ALT) less than three times normal,
  • Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
  • Patients of both genders must be willing to practice effective birth control during this trial because the potential for teratogenic effects are unknown.
  • Patients may have had prior adjuvant treatment with immunotherapy, including interferon, as long as 3 weeks have elapsed since prior systemic therapy.

You may not qualify if:

  • Patients will be excluded:
  • Who have ocular or mucosal melanoma.
  • Who are undergoing or have undergone in the past 3 weeks any systemic therapy except surgery for their cancer, and must have recovered to a grade I from any adverse effects of treatment prior to entry, other than those that do not have clinical implications, e.g. vitiligo, alopecia.
  • Have active systemic infections, autoimmune disease or any known immunodeficiency disease.
  • Who require systemic steroid therapy.
  • Who are pregnant (because of possible side effects on the fetus) or breastfeeding because of unknown effects on the developing child).
  • Who are known to be positive for hepatitis BsAG or human immunodeficiency virus (HIV) antibody (because of possible immune effects of these conditions).
  • Who have any form of autoimmune disease (such as autoimmune colitis or Crohn's Disease) or immunodeficiency as evidenced by abnormal white blood count (WBC) count 8 and/or presence of opportunistic infections. Must have recovered immune competence after radiation therapy. (The experimental treatment being evaluated in this protocol depends on an intact immune system. Patients who have decreased immune competence may be less responsive to the experimental treatment and more susceptible to its toxicities.)
  • Who have previously been immunized with gp100.
  • Who have known hypersensitivity to any of the agents used in this study.
  • Who have previously received chemotherapy for treatment of melanoma.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

National Cancer Institute (NCI)

Bethesda, Maryland, 20892, United States

Location

Related Publications (1)

  • Kawakami Y, Eliyahu S, Delgado CH, Robbins PF, Rivoltini L, Topalian SL, Miki T, Rosenberg SA. Cloning of the gene coding for a shared human melanoma antigen recognized by autologous T cells infiltrating into tumor. Proc Natl Acad Sci U S A. 1994 Apr 26;91(9):3515-9. doi: 10.1073/pnas.91.9.3515.

    PMID: 8170938BACKGROUND

Related Links

MeSH Terms

Conditions

Melanoma

Interventions

montanide ISA 51Imiquimod

Condition Hierarchy (Ancestors)

Neuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeNeoplasmsNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsNeoplasms by SiteSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

AminoquinolinesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Steven A. Rosenberg, M.D.
Organization
National Cancer Institute, National Institutes of Health

Study Officials

  • Steven A Rosenberg, M.D.

    National Cancer Institute, National Institutes of Health

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Dr. Steven Rosenberg

Study Record Dates

First Submitted

January 7, 2006

First Posted

January 9, 2006

Study Start

January 1, 2006

Primary Completion

May 1, 2010

Study Completion

May 1, 2010

Last Updated

October 19, 2012

Results First Posted

August 14, 2012

Record last verified: 2012-10

Locations