NCT00239148

Brief Summary

The purpose of the study is to determine whether E1 and G1 are safe and effective in the treatment of type 1 diabetes. Type 1 diabetes is an autoimmune disease, in which the immune system attacks pancreatic beta cells. These cells produce insulin, which regulates blood glucose. The mainstay of current treatment for type 1 diabetes is dietary control and daily parenteral administration of insulin. Recent diabetes research has increasingly focused on pancreatic islet cell replacement, either by islet cell transplantation or by endogenous regeneration of islet cells. During fetal development, islet precursor cells proliferate and differentiate into mature beta cells capable of producing insulin. This process is known as islet cell neogenesis. Islet cell neogenesis normally ceases around birth, however, the adult pancreas still retains significant potential for islet regeneration, as shown by tissue repair following pancreatic injury. Pre-clinical studies have shown that E1 and G1 can re-establish islet cell neogenesis and increase pancreatic insulin production in diabetic animal models. It is therefore postulated that treatment with E1 and G1 may produce islet cell regeneration in type 1 diabetic patients.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Jun 2005

Geographic Reach
1 country

5 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2005

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

October 12, 2005

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 14, 2005

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2006

Completed
Last Updated

October 18, 2019

Status Verified

October 1, 2019

First QC Date

October 12, 2005

Last Update Submit

October 17, 2019

Conditions

Keywords

Type 1 diabetes

Outcome Measures

Primary Outcomes (1)

  • To evaluate the safety and tolerability of repeated subcutaneous doses of E1 in combination with G1 in patients with type 1 diabetes

Secondary Outcomes (1)

  • To evaluate the pharmacokinetic (PK) profile and clinical effects of repeated subcutaneous doses of E1 in combination with G1 in patients with type 1 diabetes

Interventions

Eligibility Criteria

Age18 Years - 40 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Clinical diagnosis Type 1 diabetes requiring treatment with insulin for a minimum of 1 year
  • On a stable insulin regimen for at least 60 days prior to screening
  • Currently self monitoring blood glucose levels at least 3 times per day
  • No episodes of severe hypoglycemia for 60 days prior to screening
  • Body mass index within the range 19-30 kg/m2
  • Patient cannot live alone during the treatment phase and up to 1 month in follow-up

You may not qualify if:

  • Known of suspected history of significant liver, or other GI disease
  • History of significant cardiovascular disease including stroke, peripheral vascular disease or any related symptoms
  • History of peptic ulcer disease and/or GI bleeding/perforation
  • History of cancer
  • History or presence of proliferative retinopathy, severe non-proliferative retinopathy, macular edema or presence of untreated diabetic eye disease
  • History of treated peripheral or autonomic neuropathy
  • Serum creatine superior or equal to 2.0 mg/dL
  • History of hypoglycemia unawareness
  • Non-healed diabetic ulcer

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (5)

Pinnacle Research Group

Anniston, Alabama, 36207, United States

Location

Diablo Clinical Research

Walnut Creek, California, 94598, United States

Location

Diabetes - Endocrinology Center of West New York

Buffalo, New York, 14209, United States

Location

Highgate Specialty Center

Durham, North Carolina, 27713, United States

Location

Diabetes and Glandular Disease Research Associates

San Antonio, Texas, 78229-4801, United States

Location

MeSH Terms

Conditions

Diabetes Mellitus, Type 1

Interventions

methyl N-acetylsibirosaminide

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Aleksandra Pastrak, M.D.

    OPKO Health, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

October 12, 2005

First Posted

October 14, 2005

Study Start

June 1, 2005

Study Completion

December 1, 2006

Last Updated

October 18, 2019

Record last verified: 2019-10

Locations