NCT00162981

Brief Summary

The purpose of this study is to evaluate the safety and efficacy of clobazam as adjunctive therapy in the treatment of seizures which lead to drop attacks (drop seizures) in subjects 2 to 30 years of age with Lennox-Gastaut Syndrome (LGS). Subjects will be enrolled at approximately 10 investigational sites in the U.S. for up to 15 weeks. Subjects will be randomly assigned to either a low dose or a high dose. The study will include a baseline period, a titration period and a maintenance period. After the maintenance period, subjects will either continue into an open-label extension study or enter the taper period with a final visit 1 week after the last dose.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
68

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Oct 2005

Shorter than P25 for phase_2

Geographic Reach
1 country

14 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 9, 2005

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 13, 2005

Completed
18 days until next milestone

Study Start

First participant enrolled

October 1, 2005

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2006

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2006

Completed
5.4 years until next milestone

Results Posted

Study results publicly available

February 9, 2012

Completed
Last Updated

February 9, 2012

Status Verified

January 1, 2012

Enrollment Period

10 months

First QC Date

September 9, 2005

Results QC Date

November 7, 2011

Last Update Submit

January 6, 2012

Conditions

Outcome Measures

Primary Outcomes (2)

  • Percent Reduction in Number of Drop Seizures.

    Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

    4-week baseline period and 4-week maintenance period

  • A Comparison of the High Dose Group to Low Dose Group of the Percent Reduction in Number of Drop Seizures.

    Number of drop seizures (average per week) was obtained from seizure diaries. The average drop in seizures per week for patients who did not complete the maintenance period was calculated based on the time from the beginning of the maintenance period to date of withdrawal.

    4-week baseline period and the 4-week maintenance period

Secondary Outcomes (3)

  • Percent of Patients Considered Treatment Responders Defined as Those With a >= 25%, >= 50%, >= 75%, and 100% Reduction in Drop Seizures.

    4-week baseline period and 4-week maintenance period

  • Parent/Caregiver Global Evaluations of the Patient's Overall Change in Symptoms.

    Week 3

  • Parent/Caregiver Global Evaluations of the Patient's Overall Change in Symptoms.

    Week 7

Study Arms (2)

Clobazam Low Dose

EXPERIMENTAL
Drug: Clobazam Low Dose

Clobazam High Dose

EXPERIMENTAL
Drug: Clobazam High Dose

Interventions

5 to 10 mg/day with doses in the morning and at bedtime; orally

Also known as: Onfiâ„¢
Clobazam Low Dose

5 to 40 mg/day with doses in the morning and at bedtime; orally

Also known as: Onfiâ„¢
Clobazam High Dose

Eligibility Criteria

Age2 Years - 30 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Subject must have been \<11 years of age at the onset of LGS
  • Subject must have LGS
  • Subject must be on at least 1 stable dose AED
  • Parent or caregiver must be able to keep an accurate seizure diary

You may not qualify if:

  • Etiology of subject's seizures is a progressive neurologic disease. Subjects with tuberous sclerosis will not be excluded from study participation
  • Subject has had an episode of status epilepticus within 12 weeks of baseline
  • Subject has had an anoxic episode requiring resuscitation within 1 year of screening
  • Subject has had a clinically significant history of an allergic reaction or significant sensitivity to benzodiazepines
  • Subject is taking more than 3 concurrent AEDs. Note: Vagal Nerve Stimulation (VNS) or ketogenic diet is allowed and each will be counted as one of the three allowed AEDs
  • If the subject is on the ketogenic diet, has been for less than 4 weeks prior to screening or suffers from frequent stooling
  • If the subject has a VNS, the settings have not been stable for at least 4 weeks prior to screening
  • Subject has taken corticotropins in the 6 months prior to screening
  • Subject is currently taking long-term systemic steroids (excluding inhaled medication for asthma treatment) or any other daily medication known to exacerbate epilepsy. An exception will be made of prophylactic medication, for example, for urinary tract infections or asthma
  • If the subject is taking felbamate, has been taking it for less than 1 year prior to screening or previous treatment with felbamate resulted in withdrawal due to liver or bone marrow adverse events

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

Barrow Neurological Institute

Phoenix, Arizona, 85013, United States

Location

Childrens Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Pediatric Epilepsy & Neurology Specialists

Tampa, Florida, 33609, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Childrens Hospital Boston

Boston, Massachusetts, 02115, United States

Location

Minnesota Epilepsy Group, P.A.

Saint Paul, Minnesota, 55102, United States

Location

Children's Hospital

Columbus, Ohio, 43205, United States

Location

University of Tennessee Health Science Center

Memphis, Tennessee, 38105, United States

Location

Dallas Pediatric Neurology Associates

Dallas, Texas, 75230, United States

Location

Texas Child Neurology, LLP

Plano, Texas, 75075, United States

Location

Monarch Medical Research

Norfolk, Virginia, 23510, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23298, United States

Location

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, 53201, United States

Location

Related Publications (1)

  • Conry JA, Ng YT, Paolicchi JM, Kernitsky L, Mitchell WG, Ritter FJ, Collins SD, Tracy K, Kormany WN, Abdulnabi R, Riley B, Stolle J. Clobazam in the treatment of Lennox-Gastaut syndrome. Epilepsia. 2009 May;50(5):1158-66. doi: 10.1111/j.1528-1167.2008.01935.x. Epub 2008 Dec 15.

    PMID: 19170737BACKGROUND

MeSH Terms

Conditions

EpilepsyEpilepsy, GeneralizedSeizures

Interventions

Clobazam

Condition Hierarchy (Ancestors)

Brain DiseasesCentral Nervous System DiseasesNervous System DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

BenzodiazepinesBenzazepinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Email contact via H. Lundbeck A/S
Organization
Lundbeck LLC

Study Officials

  • Email contact via H. Lundbeck A/S

    LundbeckClinicalTrials@lundbeck.com

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 9, 2005

First Posted

September 13, 2005

Study Start

October 1, 2005

Primary Completion

August 1, 2006

Study Completion

October 1, 2006

Last Updated

February 9, 2012

Results First Posted

February 9, 2012

Record last verified: 2012-01

Locations