NCT00063583

Brief Summary

The purpose of this study is to determine whether a new investigational drug, pirfenidone, will be an effective therapy for diabetic patients with kidney dysfunction. Our hypothesis is that administration of pirfenidone to type 1 and type 2 diabetic patients with advanced kidney disease will lead to preservation of kidney function.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
77

participants targeted

Target at P75+ for phase_1 diabetes-mellitus

Timeline
Completed

Started Jun 2003

Longer than P75 for phase_1 diabetes-mellitus

Geographic Reach
1 country

3 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2003

Completed
29 days until next milestone

First Submitted

Initial submission to the registry

June 30, 2003

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 2, 2003

Completed
4.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2007

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2009

Completed
Last Updated

November 4, 2009

Status Verified

November 1, 2009

Enrollment Period

4.4 years

First QC Date

June 30, 2003

Last Update Submit

November 3, 2009

Conditions

Keywords

Kidney disease

Outcome Measures

Primary Outcomes (1)

  • The primary endpoint will be the change in renal function from baseline to the end of the study period (12 months).

    12 months

Secondary Outcomes (3)

  • % change in urine albumin excretion from baseline to end of study period.

    12 months

  • % change in levels of TGF-b1 in urine, plasma and serum from baseline to end of study period.

    12 months

  • • Determine the relationship between % change in TGF-b1 levels and the change in GFR

    12 months

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Placebo

Drug: Pirfenidone

Pirfenidone 1200 mg/day

EXPERIMENTAL

Pirfenidone will be administered at a dose of 1200 mg/day

Drug: Pirfenidone

Pirfenidone 2400 mg/day

EXPERIMENTAL

Pirfenidone will be administered at 2400 mg/day

Drug: Pirfenidone

Interventions

Pirfenidone will be administered orally at 1200 or 2400 mg day in divided doses

Pirfenidone 1200 mg/dayPirfenidone 2400 mg/dayPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Type 1 or type 2 diabetes
  • Males and females greater than or equal to 18 years.
  • Abnormal kidney function determined by glomerular filtration rate
  • History of proteinuria
  • Blood pressure controlled to \<140/90 on anti-hypertensive medication

You may not qualify if:

  • Cancer, liver disease, hepatitis, HIV+
  • History of heart attack, unstable angina, stroke or peptic ulcer in the past 6 months
  • Pregnant or planning to become pregnant during the study period
  • Other known kidney disease besides diabetic nephropathy
  • Expect to begin dialysis or receive a kidney transplant within 1 year of study enrollment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

National Institute of Diabetes and Digestive and Kidney Disease (NIDDK)

Bethesda, Maryland, 20892, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

The Center for Diabetic Kidney Disease at Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

Related Publications (6)

  • Sharma K, Ziyadeh FN, Alzahabi B, McGowan TA, Kapoor S, Kurnik BR, Kurnik PB, Weisberg LS. Increased renal production of transforming growth factor-beta1 in patients with type II diabetes. Diabetes. 1997 May;46(5):854-9. doi: 10.2337/diab.46.5.854.

    PMID: 9133555BACKGROUND
  • Shimizu F, Fukagawa M, Yamauchi S, Taniyama M, Komemushi S, Margolin SB, Kurokawa K: Pirfenidone prevents the progression of irreversible glomerular sclerotic lesions in rats. Nephrology 3:315-322, 1997

    BACKGROUND
  • Shimizu T, Fukagawa M, Kuroda T, Hata S, Iwasaki Y, Nemoto M, Shirai K, Yamauchi S, Margolin SB, Shimizu F, Kurokawa K. Pirfenidone prevents collagen accumulation in the remnant kidney in rats with partial nephrectomy. Kidney Int Suppl. 1997 Dec;63:S239-43.

    PMID: 9407470BACKGROUND
  • Iyer SN, Gurujeyalakshmi G, Giri SN. Effects of pirfenidone on transforming growth factor-beta gene expression at the transcriptional level in bleomycin hamster model of lung fibrosis. J Pharmacol Exp Ther. 1999 Oct;291(1):367-73.

    PMID: 10490926BACKGROUND
  • McGowan T, Dunn SR, Sharma K: Treatment of db/db mice with pirfenidone leads to improved histology and serum creatinine. J Am Soc Nephrology 11:A2814, 2000

    BACKGROUND
  • Raghu G, Johnson WC, Lockhart D, Mageto Y. Treatment of idiopathic pulmonary fibrosis with a new antifibrotic agent, pirfenidone: results of a prospective, open-label Phase II study. Am J Respir Crit Care Med. 1999 Apr;159(4 Pt 1):1061-9. doi: 10.1164/ajrccm.159.4.9805017.

    PMID: 10194146BACKGROUND

MeSH Terms

Conditions

Diabetes MellitusDiabetic NephropathiesKidney Diseases

Interventions

pirfenidone

Condition Hierarchy (Ancestors)

Glucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesDiabetes Complications

Study Officials

  • Kumar Sharma, M.D.

    UCSD

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDIV

Study Record Dates

First Submitted

June 30, 2003

First Posted

July 2, 2003

Study Start

June 1, 2003

Primary Completion

November 1, 2007

Study Completion

March 1, 2009

Last Updated

November 4, 2009

Record last verified: 2009-11

Locations