NCT00056550

Brief Summary

Patients with hereditary antithrombin (AT) deficiency are at increased risk of venous thrombosis and pulmonary embolism, particularly during certain high risk procedures. The trial is focusing on patients with confirmed hereditary antithrombin deficiency who are undergoing a surgical procedure or induced/spontaneous labor and delivery. The study will test the safety and efficacy of recombinant human antithrombin (rhAT) by infusing rhAT prior to, during and following the period of risk or surgical procedure.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
14

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Dec 2002

Shorter than P25 for phase_3

Geographic Reach
6 countries

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2002

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

March 17, 2003

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 18, 2003

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2004

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2004

Completed
8.7 years until next milestone

Results Posted

Study results publicly available

October 16, 2012

Completed
Last Updated

October 16, 2012

Status Verified

August 1, 2012

Enrollment Period

1.2 years

First QC Date

March 17, 2003

Results QC Date

March 19, 2012

Last Update Submit

September 17, 2012

Conditions

Keywords

Antithrombin Deficiency, CongenitalAntithrombin III Deficiency

Outcome Measures

Primary Outcomes (1)

  • Incidence of Thromboembolic Events Acute Deep Venous Thrombosis (DVT) and/or Thromboembolic Events Other Than Acute Deep Vein Thrombosis (DVT).

    Observation for clinical signs and symptoms of thromboembolic events are evaluated for acute deep vein thrombosis (DVT) using duplex ultrasonography and/or other imaging tests to confirm clinical signs/symptoms. Duplex ultrasonography was performed at baseline, last day of dosing and day 7 (+ or -1 day).

    Baseline, last day of dosing and day 7 (+ or - 1 day)

Secondary Outcomes (1)

  • Local Assessment of Thromboembolism by Physical Examination.

    30 days after last dose

Study Arms (1)

Recombinant Human Antithrombin (rhAT) infusion

EXPERIMENTAL

Loading and continuous infusion dose of rhAT to target and maintain an AT activity level \> 80% and \< 120% of normal.

Biological: Recombinant Human Antithrombin (rhAT)

Interventions

Biological/Vaccine: Recombinant human antithrombin(rhAT) Phase III clinical trial.

Also known as: ATryn
Recombinant Human Antithrombin (rhAT) infusion

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Have congenital AT deficiency with a personal or family history of venous thrombotic events.
  • Have a history of congenital AT deficiency that includes 2 or more plasma AT activity levels of ≤ 60% normal.
  • Are scheduled to have an elective procedure known to be associated with a high risk for occurrence of Deep Venous Thrombosis (DVT). This will include surgical patients or pregnant patients scheduled for cesarean section or delivery induction. In addition, hospitalized pregnant HD patients in active labor will be allowed into the study.
  • Are at least 18 years of age, not exceeding 70 years of age.
  • Have signed an informed consent form.
  • Have a negative serum pregnancy test at screening and negative urine pregnancy test at baseline. This only applies to female surgical patients (not scheduled for cesarean section) of childbearing potential.
  • Are able to comply with the requirements of the study protocol.

You may not qualify if:

  • Patients who have a diagnosis of hereditary APC resistance, Factor V Leiden, Protein S or C deficiency, prothrombin gene mutation (G20210A), or acquired (lupus anticoagulant) thrombophilic disorder.
  • Patients who are scheduled for a neurosurgical procedure or open-heart surgery.
  • Patients who have an underlying medical condition, which in the opinion of the investigator, could complicate the assessment of the incidence of DVT.
  • Patients who have a known allergy to goats or goat products.
  • Patients who have participated in a study employing an investigational drug within 30 days of the start of their participation in the current trial.
  • Patients using fondaparinux sodium, or are expected to be treated with fondaparinux sodium during the study period.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Unknown Facility

Marietta, Georgia, United States

Location

Unknown Facility

Charleston, South Carolina, United States

Location

Unknown Facility

Paris, France

Location

Unknown Facility

Toulouse, France

Location

Unknown Facility

Berlin, Germany

Location

Unknown Facility

Hanover, Germany

Location

Unknown Facility

Mannheim, Germany

Location

Unknown Facility

Milan, Italy

Location

Unknown Facility

Stockholm, Sweden

Location

Unknown Facility

Bristol, United Kingdom

Location

Unknown Facility

Manchester, United Kingdom

Location

Related Publications (1)

  • DeJongh J, Frieling J, Lowry S, Drenth HJ. Pharmacokinetics of recombinant human antithrombin in delivery and surgery patients with hereditary antithrombin deficiency. Clin Appl Thromb Hemost. 2014 May;20(4):355-64. doi: 10.1177/1076029613516188. Epub 2013 Dec 11.

Related Links

MeSH Terms

Conditions

Antithrombin III Deficiency

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesBlood Protein DisordersThrombophiliaGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Results Point of Contact

Title
Denise Tilton, RN, MHA, Director Clinical Development
Organization
GTC Biotherapeutics

Study Officials

  • Cambell Tait, MD

    Royal Infirmary Glaskow

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
PREVENTION
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 17, 2003

First Posted

March 18, 2003

Study Start

December 1, 2002

Primary Completion

February 1, 2004

Study Completion

February 1, 2004

Last Updated

October 16, 2012

Results First Posted

October 16, 2012

Record last verified: 2012-08

Locations