NCT00054613

Brief Summary

The purpose of this study is to determine whether extracorporeal photoimmune therapy with UVADEX (ECP) added to standard therapy is effective in the treatment of chronic graft-versus-host disease (GvHD).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
72

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jun 2002

Geographic Reach
11 countries

30 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2002

Completed
8 months until next milestone

First Submitted

Initial submission to the registry

February 5, 2003

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 6, 2003

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2004

Completed
Last Updated

August 16, 2017

Status Verified

August 1, 2017

First QC Date

February 5, 2003

Last Update Submit

August 14, 2017

Conditions

Keywords

Graft-versus-Host DiseaseExtracorporeal Photopheresis

Interventions

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Documented skin disease classical for chronic GvHD (e.g. hypopigmentation, hyperpigmentation, lichenoid lesions, sclerodermatous lesions)greater than or equal to 100 days post transplantation.
  • Patients with documented chronic GvHD that is corticosteroid refractory, corticosteroid dependent or corticosteroid intolerant.
  • Women of childbearing potential must agree to use a reliable method of birth control for the duration of this study.
  • Patients must weight at least 40 kg (88 lbs.)

You may not qualify if:

  • Active gastrointestinal bleeding
  • Previous treatment with ECP
  • Females who are pregnant and/or lactating

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (31)

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Rush Presbyterian - St. Lukes Medical Center

Chicago, Illinois, 60612, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Tufts New England Medical Center

Boston, Massachusetts, 02111, United States

Location

Brigham and Womens

Boston, Massachusetts, 02115, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109-0914, United States

Location

Kansas City Cancer Center

Kansas City, Missouri, 64111, United States

Location

University of Nebraska

Omaha, Nebraska, 68198-7680, United States

Location

Jewish Hospital

Cincinnati, Ohio, 45236, United States

Location

Fred Hutchinson Cancer Research Center

Seattle, Washington, 19024, United States

Location

St. Vincent's Hospital

Darlinghurst, New South Wales, 2010, Australia

Location

Peter MacCallum

East Melbourne, Australia

Location

Alfred Hospital

Melbourne, Australia

Location

Royal Melbourne Hospital

Parkville, 3050, Australia

Location

General Hospital of Vienna

Vienna, A-1090, Austria

Location

Hopital Edouard Herriot

Lyon, 69437, France

Location

Hopital Pitie-Salpetriere

Paris, F-75013, France

Location

University of Dresden

Dresden, D-01307, Germany

Location

Universitatis Hautklinik

Essen, 45122, Germany

Location

Universitatsklinikum Leipzig AOR

Leipzig, D-04103, Germany

Location

Ludwig-Maximilians-Universitaet Muenchen

München, D-81377, Germany

Location

Careggi Hospital

Florence, 1-50134, Italy

Location

San Martino Hospital

Genova, 16132, Italy

Location

Instituto Portugues de Oncologia de Francisco Gentil

Lisbon, 1099-023, Portugal

Location

Klinika hematologie a transfuziologie FN

Bratislava, 81103, Slovakia

Location

Hospital dela Santa Creu i Sant Pau. Universitat Autonoma de Barcelona

Barcelona, E-08025, Spain

Location

Kantonsspital Basel

Basel, CH-4031, Switzerland

Location

Ankara University Medical School

Altındağ, Ankara, 6100, Turkey (Türkiye)

Location

Rotherham General Hospital

Rotherham, Yorkshire, S60 2UD, United Kingdom

Location

Glasgow Royal Infirmary

Glasgow, G4 OS4, United Kingdom

Location

Related Publications (3)

  • Smith EP, Sniecinski I, Dagis AC, Parker PM, Snyder DS, Stein AS, Nademanee A, O'Donnell MR, Molina A, Schmidt GM, Stepan DE, Kapoor N, Niland JC, Forman SJ. Extracorporeal photochemotherapy for treatment of drug-resistant graft-vs.-host disease. Biol Blood Marrow Transplant. 1998;4(1):27-37. doi: 10.1016/s1083-8791(98)90007-6.

    PMID: 9701389BACKGROUND
  • Greinix HT, Volc-Platzer B, Knobler RM. Extracorporeal photochemotherapy in the treatment of severe graft-versus-host disease. Leuk Lymphoma. 2000 Feb;36(5-6):425-34. doi: 10.3109/10428190009148389.

    PMID: 10784386BACKGROUND
  • Flowers ME, Apperley JF, van Besien K, Elmaagacli A, Grigg A, Reddy V, Bacigalupo A, Kolb HJ, Bouzas L, Michallet M, Prince HM, Knobler R, Parenti D, Gallo J, Greinix HT. A multicenter prospective phase 2 randomized study of extracorporeal photopheresis for treatment of chronic graft-versus-host disease. Blood. 2008 Oct 1;112(7):2667-74. doi: 10.1182/blood-2008-03-141481. Epub 2008 Jul 11.

MeSH Terms

Conditions

Graft vs Host Disease

Interventions

MethoxsalenPhotopheresis

Condition Hierarchy (Ancestors)

Immune System Diseases

Intervention Hierarchy (Ancestors)

FurocoumarinsCoumarinsBenzopyransPyransHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds, 3-RingPUVA TherapyUltraviolet TherapyPhototherapyTherapeuticsExtracorporeal CirculationSurgical Procedures, Operative

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

February 5, 2003

First Posted

February 6, 2003

Study Start

June 1, 2002

Study Completion

March 1, 2004

Last Updated

August 16, 2017

Record last verified: 2017-08

Locations