NCT00047723

Brief Summary

The purpose of this trial is to test the safety, tolerability, and effectiveness of minocycline compared to placebo in patients with amyotrophic lateral sclerosis (ALS).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
400

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jan 2003

Typical duration for phase_3

Geographic Reach
1 country

30 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 16, 2002

Completed
1 day until next milestone

First Posted

Study publicly available on registry

October 17, 2002

Completed
3 months until next milestone

Study Start

First participant enrolled

January 1, 2003

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2007

Completed
Last Updated

December 21, 2007

Status Verified

December 1, 2007

First QC Date

October 16, 2002

Last Update Submit

December 18, 2007

Conditions

Keywords

ALSamyotrophic lateral sclerosisminocycline

Outcome Measures

Primary Outcomes (1)

  • Change in function as detected by the ALS Functional Rating Scale (ALSFRS-R) in patients taking minocycline compared to those taking placebo.

Secondary Outcomes (1)

  • Changes in manual muscle testing (MMT), forced vital capacity (FVC, percent predicted), quality of life (QOL) and survival

Interventions

Eligibility Criteria

Age21 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • A clinical diagnosis of laboratory-supported probable, probable or definite ALS, according to modified EL Escorial criteria.
  • FVC greater or equal to 75% of predicted.
  • Onset of weakness within 3 years prior to enrollment.
  • If patients are receiving riluzole they must be on a stable dose for at least the past thirty days.
  • Women of childbearing age must be non-lactating and surgically sterile or using an effective method of birth control and have a negative pregnancy test (adequate birth control includes use of intra-uterine device or oral contraceptives plus a barrier method, e.g. condom, diaphragm).
  • Willing and able to give signed informed consent that has been approved by your Institutional Review Board (IRB).

You may not qualify if:

  • Requirement for tracheotomy ventilation (or non-invasive ventilation \> 23 hours/day).
  • Diagnosis of other neurodegenerative diseases (Parkinson's disease, Alzheimer's disease, etc).
  • FVC \< 75% of predicted.
  • A clinically significant history of unstable medical illness (unstable angina, advanced cancer, etc) over the last 30 days.
  • History of renal disease (screening creatinine greater than 1.5).
  • History of liver disease (screening alanine aminotransferase greater than 3 times the upper limit of normal).
  • History of hematologic disease (screening white blood cell count less than 3,800/mm3).
  • History of system lupus erythematosis (or screening ANA of 1:160 or greater).
  • Treatment with any medications that may cause lupus-like symptoms within 4 weeks of baseline visit (e.g. procainamide, hydralazine).
  • History of vestibular disease (excluding benign position vertigo).
  • Pregnancy or lactation.
  • Allergy to tetracycline antibiotics.
  • Use of minocycline within thirty days of enrollment (baseline visit).
  • Use of anti-epileptic medications other than gabapentin.
  • Limited mental capacity rendering the subject unable to provide written informed consent or comply with evaluation procedures.
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (30)

Mayo Clinic

Scottsdale, Arizona, United States

Location

University of California, Irvine

Irvine, California, United States

Location

University of California Department of Neurology

Los Angeles, California, United States

Location

California Pacific Medical Center

San Francisco, California, United States

Location

Univ. of Colorado Health Sciences Center

Denver, Colorado, United States

Location

Mayo Clinic

Jacksonville, Florida, United States

Location

University of Illinois

Chicago, Illinois, United States

Location

Indiana University School of Medicine

Indianapolis, Indiana, United States

Location

University of Iowa

Iowa City, Iowa, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, United States

Location

University of Kentucky

Lexington, Kentucky, United States

Location

Hennepin County Med Center

Minneapolis, Minnesota, United States

Location

University of Minnesota

Minneapolis, Minnesota, United States

Location

Washington University

St Louis, Missouri, United States

Location

UMDNJ/Robert Wood Johnson Medical Center

New Brunswick, New Jersey, United States

Location

University of New Mexico

Albuquerque, New Mexico, United States

Location

Columbia Unversity, Eleanor and Lou Gehrig MDA/ALS Center

New York, New York, 10032, United States

Location

Carolinas Medical Center

Charlotte, North Carolina, United States

Location

Duke University

Durham, North Carolina, United States

Location

Wake Forest University

Winston-Salem, North Carolina, United States

Location

Metro Health Clinic

Cleveland, Ohio, United States

Location

Oregon Health & Science University

Portland, Oregon, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Drexel University College of Medicine, Hahnemann Campus

Philadelphia, Pennsylvania, United States

Location

University of Texas Southwestern

Dallas, Texas, United States

Location

Methodist Hospital

Houston, Texas, United States

Location

University of Texas Health Sciences Center

San Antonio, Texas, United States

Location

University of Utah

Salt Lake City, Utah, United States

Location

University of Vermont

Burlington, Vermont, United States

Location

Virginia Mason Medical Center

Seattle, Washington, United States

Location

Related Publications (1)

  • Gordon PH, Moore DH, Miller RG, Florence JM, Verheijde JL, Doorish C, Hilton JF, Spitalny GM, MacArthur RB, Mitsumoto H, Neville HE, Boylan K, Mozaffar T, Belsh JM, Ravits J, Bedlack RS, Graves MC, McCluskey LF, Barohn RJ, Tandan R; Western ALS Study Group. Efficacy of minocycline in patients with amyotrophic lateral sclerosis: a phase III randomised trial. Lancet Neurol. 2007 Dec;6(12):1045-53. doi: 10.1016/S1474-4422(07)70270-3. Epub 2007 Nov 5.

MeSH Terms

Conditions

Amyotrophic Lateral Sclerosiscyclopia sequence

Interventions

Minocycline

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesMotor Neuron DiseaseNeurodegenerative DiseasesTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

TetracyclinesNaphthacenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic Compounds

Study Officials

  • Paul H. Gordon, M.D.,

    Associate Medical Director, Eleanor and Lou Gehrig MDA/ALS Center, Columbia University Medical Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Purpose
TREATMENT
Sponsor Type
NIH

Study Record Dates

First Submitted

October 16, 2002

First Posted

October 17, 2002

Study Start

January 1, 2003

Study Completion

January 1, 2007

Last Updated

December 21, 2007

Record last verified: 2007-12

Locations