NCT00041938

Brief Summary

The purpose of this study is to determine which of two treatments, Warfarin or aspirin, is better for preventing death and stroke in patients with poor heart function. We are now transitioning into the sub-analysis part of the WARCEF patient data. The study has recently completed data analysis for its Primary Aim. All randomized patients have completed their follow up. All study related procedure as per the protocol has been completed. We are now in the extension phase of the study to obtain more patient data to address further aims of the study. No new procedures are performed and data already in place at the sites will be collected (EKG and echocardiograms). The aims for this study extension are:

  • To assess progression of cardiac dysfunction over time among heart failure patients
  • To correlate prognosis with cardiac dysfunction

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2,305

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2002

Longer than P75 for phase_3

Geographic Reach
2 countries

64 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 19, 2002

Completed
3 days until next milestone

First Posted

Study publicly available on registry

July 22, 2002

Completed
2 months until next milestone

Study Start

First participant enrolled

October 1, 2002

Completed
8.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2011

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

May 14, 2013

Completed
1.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2014

Completed
Last Updated

September 5, 2014

Status Verified

August 1, 2014

Enrollment Period

8.8 years

First QC Date

July 19, 2002

Results QC Date

January 3, 2013

Last Update Submit

August 29, 2014

Conditions

Keywords

heart diseasestrokeischemic heart diseasemyocardial infarctionatrial fibrillationlow ejection fractioncardiac failureaspirinWarfarinanticoagulant

Outcome Measures

Primary Outcomes (1)

  • Event Rate Per 100 Patient Years for Composite Endpoint of Ischemic Stroke, Intracerebral Hemorrhage, or Death

    The time, in years, from randomization to the first to occur of ischemic stroke, intracerebral hemorrhage, or death, up to a maximum of 6 years. Event rate per 100 patient years = 100\*(number of subjects with event)/patient-years of follow-up. Patient years of follow-up = sum(date of conclusion of follow-up - date of randomization + 1) of all randomized patients / 365.25.

    From date of randomization until the date of the first to occur of ischemic stroke, intracerebral hemorrhage, or death, up to 6 years

Secondary Outcomes (1)

  • Event Rate Per 100 Patient-years for Composite Endpoint of Hospitalization for Heart Failure, Myocardial Infarction, Ischemic Stroke, Intracerebral Hemorrhage, or Death.

    From randomization to the first to occur of hospitalization for heart failure, myocardial infarction, ischemic stroke, intracerebral hemorrhage, or death, up to a maximum of 6 years.

Other Outcomes (10)

  • Event Rate Per 100 Patient-years for Ischemic Stroke

    From date of randomization to date of ischemic stroke component of primary composite outcome, up to 6 years

  • Event Rate Per 100 Patient-years for Intracerebral Hemorrhage

    From date of randomization to date of intracerebral hemorrhage component of primary composite outcome, up to 6 years

  • Event Rate Per 100 Patient-years for Death

    From date of randomization to date of death component of primary composite outcome, up to 6 years

  • +7 more other outcomes

Study Arms (2)

aspirin

ACTIVE COMPARATOR

Aspirin: 325 mg per day

Drug: aspirin

warfarin

ACTIVE COMPARATOR

Warfarin: International Normalized Ratio (INR) 2.5-3.0; target INR 2.75

Drug: Warfarin

Interventions

325 mg per day

aspirin

INR 2.5-3.0; target INR 2.75

warfarin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Cardiac EF \<=35% by radionuclide ventriculography, left ventriculography or quantitive echocardiographic measurement or an echocardiographic Wall Motion Index of \<=1.2, within three months of enrollment. The patient's clinical cardiac state at enrollment should be similar to their state at the time of the qualifying echocardiogram. The qualifying left ventricular function measurement must be obtained at least three months after an MI, coronary bypass grafting, PTCA, and at least one month after pacemaker insertion. Patients scheduled for mitral valve repair should have qualifying echo after surgery.
  • Modified Rankin score \<=4.
  • Patient must be taking ACE inhibitors. If intolerant of ACE inhibitor, patient must be on angiotensin II receptor blockers or hydralazine and nitrates.
  • Patient is able to follow an outpatient protocol (requiring monthly blood tests and clinic visits every four months for the duration of the study) and is available by telephone.
  • Patient understands the purpose and requirements of the study, can make him/herself understood, and has provided informed consent.
  • Patients with recent stroke or TIA within twelve (12) months will be eligible to be included in the recent stroke (RS) subgroup.
  • Chronic CHF patients (NYHA I \* IV) admitted to the hospital can be randomized prior to discharge if the patient is stable, taking oral medications for 24 hours and ambulatory at the time of discharge. Stable New York Heart Association Class IV patients will be eligible for randomization.

You may not qualify if:

  • The presence of any of the following unequivocal cardiac sources of embolism: chronic or paroxysmal AF, mechanical valve, endocarditis, intracardiac mobile or pedunculated thrombus, and valvular vegetation.
  • Cyanotic congenital heart disease, Eisenmenger's syndrome.
  • Decompensated heart failure.
  • Cardiac surgery, angioplasty, or MI within the past 3 months prior to randomization.
  • A contraindication to the use of either warfarin or aspirin, e.g. active peptic ulcer disease, active bleeding diathesis, platelets \<100,000\*, hematocrit \<30, INR \>1.3 (if not on warfarin), clotting factor abnormality that increases the risk of bleeding, alcohol or substance abuse, severe gait instability, cerebral hemorrhage, systemic hemorrhage within the past year, severe liver impairment (AST \>3x normal\*, cirrhosis), any condition requiring regular use of non-steroidal anti-inflammatory agents, allergy to aspirin or warfarin, uncontrolled severe hypertension (systolic pressure \>180 mm Hg or diastolic pressure \> 110 mm Hg), positive stool guaiac not attributable to hemorrhoids, creatinine \>3.0\*. \*on most recent test done within 30 days prior to randomization
  • Patient needs continuing therapy with intravenous heparin or low molecular weight heparin or a specific antiplatelet agent.
  • Dementia or psychiatric or physical problem that prevents the patient from following an outpatient program reliably.
  • Comorbid conditions that may limit survival to less than five years.
  • Pregnancy, or female of childbearing potential who is not sterilized or is not using a medically accepted form of contraception\* (see procedure manual). \*A pregnancy test is required for all women of childbearing age.
  • Enrollment in another study that would conflict with WARCEF.
  • Hospitalization for new diagnosis of onset CHF within the past one month or carotid endarterectomy or pacemaker insertion within the past one month prior to randomization .
  • Person under 18 years of age.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (64)

Southern Arizona Veterans Affairs Medical Center

Tucson, Arizona, United States

Location

University of Arizona Health Sciences Center

Tucson, Arizona, United States

Location

Santa Clara Medical Center

Santa Clara, California, United States

Location

West Los Angeles Veterans Affairs Medical Center

West Los Angeles, California, United States

Location

Denver Health Medical Center

Denver, Colorado, United States

Location

Denver Veterans Affairs Medical Center

Denver, Colorado, United States

Location

George Washington University

Washington D.C., District of Columbia, 20037, United States

Location

Mayo Clinic Transplant Center

Jacksonville, Florida, United States

Location

Melbourne Internal Medicine Associates

Melbourne, Florida, United States

Location

Jackson Memorial Hospital/U. of Miami

Miami, Florida, United States

Location

Mercy Research Institute

Miami, Florida, United States

Location

Cardiovascular Consultants of South Florida

Tamarac, Florida, United States

Location

Morehouse School of Medicine

Atlanta, Georgia, United States

Location

Northeast Georgia Heart Center

Gainesville, Georgia, United States

Location

University of Illinois at Chicago

Chicago, Illinois, United States

Location

Methodist Heart, Lung and Vascular Institute

Peoria, Illinois, United States

Location

University of Kentucky

Lexington, Kentucky, United States

Location

Louisville Veterans Affairs Medical Center

Louisville, Kentucky, United States

Location

University of Louisville

Louisville, Kentucky, United States

Location

Gulf Regional Research, LLC

Metairie, Louisiana, United States

Location

LSU Health Sciences Center

Shreveport, Louisiana, United States

Location

Lahey Clinic

Burlington, Massachusetts, United States

Location

Veterans Affairs Medical Center

Detroit, Michigan, United States

Location

Mercy Health Partners

Muskegon, Michigan, United States

Location

Reno Veterans Affairs Medical Center

Reno, Nevada, United States

Location

Concord Hospital

Concord, New Hampshire, United States

Location

UMDNJ - New Brunswick

New Brunswick, New Jersey, United States

Location

University of Medicine and Dentistry of New Jersey

Newark, New Jersey, United States

Location

Albany Medical College

Albany, New York, United States

Location

Buffalo General Hospital

Buffalo, New York, United States

Location

Kaleida Health Millard Fillmore Hospital

Buffalo, New York, United States

Location

Five Towns Neuroscience Research

Cedarhurst, New York, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, United States

Location

Columbia University, New York Presbyterian Hospital PH 3-342

New York, New York, 10032, United States

Location

Columbia University Medical Center

New York, New York, United States

Location

Mount Sinai Medical Center

New York, New York, United States

Location

Northport Veterans Affairs Medical Center

Northport, New York, United States

Location

University of Rochester Medical Center

Rochester, New York, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Location

MetroHealth Medical Center

Cleveland, Ohio, United States

Location

Oklahoma City Veterans Affairs Medical Center

Oklahoma City, Oklahoma, United States

Location

Lehigh Valley Hospital

Allentown, Pennsylvania, United States

Location

Tri-State Medical Group Cardiology

Beaver, Pennsylvania, United States

Location

Sewickley Valley Medical Group, Cardiology

Leetsdale, Pennsylvania, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, United States

Location

Hospital of the University of Pennsylvania

Philadelphia, Pennsylvania, United States

Location

Penn Presbyterian Medical Center

Philadelphia, Pennsylvania, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, United States

Location

Black Hills Health Care System

Fort Meade, South Dakota, United States

Location

Brooke Army Medical Center MCHE - MDC Cardiology Service

Fort Sam Houston, Texas, United States

Location

Michael E. DeBakey Veterans Affairs Medical Center-MEDVAMC

Houston, Texas, United States

Location

Salem VAMC

Salem, Virginia, United States

Location

Huntington Veterans Affairs Medical Center

Huntington, West Virginia, United States

Location

William S. Middleton Memorial Veterans Hospital

Madison, Wisconsin, United States

Location

Center for Neurologic Research

Lethbridge, Alberta, Canada

Location

St. Boniface General Hospital

Winnipeg, Manitoba, Canada

Location

Saint John Regional Hospital

Saint John, New Brunswick, Canada

Location

QE II Health Sciences Centre

Halifax, Nova Scotia, Canada

Location

London Health Sciences Centre

London, Ontario, Canada

Location

Ottawa Heart Institute

Ottawa, Ontario, Canada

Location

Etobicoke Cardiac Research Centre

Rexdale, Ontario, Canada

Location

St. Michael's Hospital

Toronto, Ontario, Canada

Location

Montreal General Hospital

Montreal, Quebec, Canada

Location

Montreal Heart Institute

Montreal, Quebec, Canada

Location

Related Publications (9)

  • Corica B, Romiti GF, Simoni AH, Mei DA, Bucci T, Thompson JLP, Qian M, Homma S, Proietti M, Lip GYH; WARCEF Investigators. Educational status affects prognosis of patients with heart failure with reduced ejection fraction: A post-hoc analysis from the WARCEF trial. Eur J Clin Invest. 2024 May;54(5):e14152. doi: 10.1111/eci.14152. Epub 2024 Jan 11.

  • Lee TC, Qian M, Liu Y, Graham S, Mann DL, Nakanishi K, Teerlink JR, Lip GYH, Freudenberger RS, Sacco RL, Mohr JP, Labovitz AJ, Ponikowski P, Lok DJ, Matsumoto K, Estol C, Anker SD, Pullicino PM, Buchsbaum R, Levin B, Thompson JLP, Homma S, Di Tullio MR; WARCEF Investigators. Cognitive Decline Over Time in Patients With Systolic Heart Failure: Insights From WARCEF. JACC Heart Fail. 2019 Dec;7(12):1042-1053. doi: 10.1016/j.jchf.2019.09.003.

  • Teerlink JR, Qian M, Bello NA, Freudenberger RS, Levin B, Di Tullio MR, Graham S, Mann DL, Sacco RL, Mohr JP, Lip GYH, Labovitz AJ, Lee SC, Ponikowski P, Lok DJ, Anker SD, Thompson JLP, Homma S; WARCEF Investigators. Aspirin Does Not Increase Heart Failure Events in Heart Failure Patients: From the WARCEF Trial. JACC Heart Fail. 2017 Aug;5(8):603-610. doi: 10.1016/j.jchf.2017.04.011.

  • Di Tullio MR, Qian M, Thompson JL, Labovitz AJ, Mann DL, Sacco RL, Pullicino PM, Freudenberger RS, Teerlink JR, Graham S, Lip GY, Levin B, Mohr JP, Buchsbaum R, Estol CJ, Lok DJ, Ponikowski P, Anker SD, Homma S; WARCEF Investigators. Left Ventricular Ejection Fraction and Risk of Stroke and Cardiac Events in Heart Failure: Data From the Warfarin Versus Aspirin in Reduced Ejection Fraction Trial. Stroke. 2016 Aug;47(8):2031-7. doi: 10.1161/STROKEAHA.116.013679. Epub 2016 Jun 28.

  • Freudenberger RS, Cheng B, Mann DL, Thompson JL, Sacco RL, Buchsbaum R, Sanford A, Pullicino PM, Levin B, Teerlink JR, Graham S, Mohr JP, Labovitz AJ, Di Tullio MR, Lip GY, Estol CJ, Lok DJ, Ponikowski P, Anker SD, Homma S; WARCEF Investigators. The first prognostic model for stroke and death in patients with systolic heart failure. J Cardiol. 2016 Aug;68(2):100-3. doi: 10.1016/j.jjcc.2015.09.014. Epub 2015 Nov 6.

  • Homma S, Thompson JL, Qian M, Ye S, Di Tullio MR, Lip GY, Mann DL, Sacco RL, Levin B, Pullicino PM, Freudenberger RS, Teerlink JR, Graham S, Mohr JP, Labovitz AJ, Buchsbaum R, Estol CJ, Lok DJ, Ponikowski P, Anker SD; WARCEF Investigators. Quality of anticoagulation control in preventing adverse events in patients with heart failure in sinus rhythm: Warfarin versus Aspirin in Reduced Cardiac Ejection Fraction trial substudy. Circ Heart Fail. 2015 May;8(3):504-9. doi: 10.1161/CIRCHEARTFAILURE.114.001725. Epub 2015 Apr 7.

  • Shaffer JA, Thompson JL, Cheng B, Ye S, Lip GY, Mann DL, Sacco RL, Pullicino PM, Freudenberger RS, Graham S, Mohr JP, Labovitz AJ, Estol CJ, Lok DJ, Ponikowski P, Anker SD, Di Tullio MR, Homma S; WARCEF Investigators. Association of quality of life with anticoagulant control in patients with heart failure: the Warfarin and Aspirin in Reduced Cardiac Ejection Fraction (WARCEF) trial. Int J Cardiol. 2014 Dec 15;177(2):715-7. doi: 10.1016/j.ijcard.2014.10.012. No abstract available.

  • Homma S, Thompson JL, Sanford AR, Mann DL, Sacco RL, Levin B, Pullicino PM, Freudenberger RS, Teerlink JR, Graham S, Mohr JP, Massie BM, Labovitz AJ, Di Tullio MR, Gabriel AP, Lip GY, Estol CJ, Lok DJ, Ponikowski P, Anker SD; WARCEF Investigators. Benefit of warfarin compared with aspirin in patients with heart failure in sinus rhythm: a subgroup analysis of WARCEF, a randomized controlled trial. Circ Heart Fail. 2013 Sep 1;6(5):988-97. doi: 10.1161/CIRCHEARTFAILURE.113.000372. Epub 2013 Jul 23.

  • Homma S, Thompson JL, Pullicino PM, Levin B, Freudenberger RS, Teerlink JR, Ammon SE, Graham S, Sacco RL, Mann DL, Mohr JP, Massie BM, Labovitz AJ, Anker SD, Lok DJ, Ponikowski P, Estol CJ, Lip GY, Di Tullio MR, Sanford AR, Mejia V, Gabriel AP, del Valle ML, Buchsbaum R; WARCEF Investigators. Warfarin and aspirin in patients with heart failure and sinus rhythm. N Engl J Med. 2012 May 17;366(20):1859-69. doi: 10.1056/NEJMoa1202299. Epub 2012 May 2.

MeSH Terms

Conditions

Heart DiseasesStrokeMyocardial IschemiaMyocardial InfarctionAtrial FibrillationHeart Failure

Interventions

AspirinWarfarin

Condition Hierarchy (Ancestors)

Cardiovascular DiseasesCerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesVascular DiseasesInfarctionIschemiaPathologic ProcessesPathological Conditions, Signs and SymptomsNecrosisArrhythmias, Cardiac

Intervention Hierarchy (Ancestors)

SalicylatesHydroxybenzoatesPhenolsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic Chemicals4-HydroxycoumarinsCoumarinsBenzopyransPyransHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Results Point of Contact

Title
Dr. J.L.P. (Seamus) Thompson
Organization
Columbia University

Study Officials

  • Shunichi Homma, M.D.

    Principal Cardiologist, Associate Chief, Division of Cardiology, and Director, Echocardiography Laboratories Professor of Medicine

    PRINCIPAL INVESTIGATOR
  • Seamus Thompson, PhD

    Statistical PI: Clinical Professor of Biostatistics and Neurology

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Margaret Milliken Hatch Professor of Medicine at the New York-Presbyterian Hospital at the Columbia University Medical Center (In Biomedical Engineering)

Study Record Dates

First Submitted

July 19, 2002

First Posted

July 22, 2002

Study Start

October 1, 2002

Primary Completion

August 1, 2011

Study Completion

July 1, 2014

Last Updated

September 5, 2014

Results First Posted

May 14, 2013

Record last verified: 2014-08

Locations