NCT00040404

Brief Summary

The purpose of this study is to establish safety for CEP-1347 and to determine an efficacious dose in the treatment of Parkinson's disease.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
806

participants targeted

Target at P75+ for phase_2 parkinson-disease

Timeline
Completed

Started Mar 2002

Typical duration for phase_2 parkinson-disease

Geographic Reach
3 countries

66 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2002

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

June 26, 2002

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 27, 2002

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2005

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2005

Completed
Last Updated

May 10, 2012

Status Verified

May 1, 2012

Enrollment Period

3.4 years

First QC Date

June 26, 2002

Last Update Submit

May 8, 2012

Conditions

Keywords

Parkinson's diseaseIdiopathic Parkinson's diseaseIdiopathic Parkinson diseaseParkinson's disease, idiopathic

Outcome Measures

Primary Outcomes (1)

  • Number of participants with disability using United Parkinson's Disease Rating Scale (UPDRS)

    Number of participants with disability sufficient to require dopaminergic therapy was assessed according to the United Parkinson's Disease Rating Scale (UPDRS) Parts I and II are historical data and are designed to rate mentation, behavior and mood; Part III is done as a motor examination at the time of a visit. The UPDRS measures patient status on a scale 0, which is normal or none, to 4, which is severe or the worst scenario.

    48 months

Secondary Outcomes (2)

  • Change from Baseline to 22 months in ([123I]β-CIT) Uptake Participants

    Change from Baseline to 22 months

  • Safety and Tolerability as assessed by the number of participants experiencing adverse events

    48 months

Study Arms (4)

CEP-1347 10mg

EXPERIMENTAL

CEP-1347 was administered at a dosage of 10mg twice daily (bid); capsule strengths were 5, 12.5, and 25 mg. Each patient took 2 capsules at each dosing time, approximately 12 hours apart, within 30 minutes after the morning and evening meals) for a total of 4 capsules per day.Patients were randomly assigned to CEP-1347 or placebo treatment in a 1:1:1:1 ratio. A blocked randomization scheme was used to ensure approximately equal numbers of patients in each of the 4 treatment groups at each center.

Drug: CEP-1347 10mg

CEP-1347 25mg

EXPERIMENTAL

CEP-1347 was administered at a dosage of 25mg twice daily (bid); capsule strengths were 5, 12.5, and 25 mg. Each patient took 2 capsules at each dosing time, approximately 12 hours apart, within 30 minutes after the morning and evening meals) for a total of 4 capsules per day.Patients were randomly assigned to CEP-1347 or placebo treatment in a 1:1:1:1 ratio. A blocked randomization scheme was used to ensure approximately equal numbers of patients in each of the 4 treatment groups at each center.

Drug: CEP1347 25mg

CEP-1347 50mg

EXPERIMENTAL

CEP-1347 was administered at a dosage of 50mg twice daily (bid); capsule strengths were 5, 12.5, and 25 mg. Each patient took 2 capsules at each dosing time, approximately 12 hours apart, within 30 minutes after the morning and evening meals) for a total of 4 capsules per day.Patients were randomly assigned to CEP-1347 or placebo treatment in a 1:1:1:1 ratio. A blocked randomization scheme was used to ensure approximately equal numbers of patients in each of the 4 treatment groups at each center.

Drug: CEP-1347 50mg

Placebo

PLACEBO COMPARATOR

Placebo capsules matching the CEP-1347 capsules were administered in the same manner.

Other: Placebo Comparator

Interventions

CEP-1347 10mg, a K252a derivative, retains neuroprotective properties

CEP-1347 10mg

CEP1347 25mg, a K252a derivative, retains neuroprotective properties

CEP-1347 25mg

CEP-1347 50mg, a K252a derivative, retains neuroprotective properties

CEP-1347 50mg

Placebo capsules matching the CEP-1347 capsules

Placebo

Eligibility Criteria

Age30 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients will be included in the study if all of the following criteria are met:
  • Willing and able to give informed consent
  • Age 30 years or older at time of diagnosis of Parkinson's disease
  • Have idiopathic Parkinson's disease with at least 2 cardinal signs of disease: resting tremor, bradykinesia, or rigidity
  • Modified Hoehn and Yahr stage less than or equal to 2.5
  • Must have had screening procedures for cancer appropriate for the patient's age and gender, within the last 12 months; or be willing to obtain such screening before randomization
  • Women: are not breastfeeding
  • Women: nonchildbearing potential (ie, postmenopausal or surgically sterile) or must use a medically accepted contraceptive regimen for at least 60 days before the baseline visit, and agree to continue such use throughout the duration of the study and for 30 days after the final dose of study drug. Women must be given a pregnancy test unless they are at least 2 years postmenopausal or surgically sterile.

You may not qualify if:

  • Patients will be excluded from participating in this study if 1 or more of the following criteria are met:
  • Have atypical Parkinsonism due to drugs, metabolic disorders, encephalitis, or other neurodegenerative diseases
  • Have confirmed diagnosis of Parkinson's disease for more than 5 years
  • Have a tremor score of 3 or more in any body part
  • Have any other known medical or psychiatric condition that may compromise participation in the study
  • Have a history of prior malignancy (excluding basal or squamous cell cancer of the skin) within the previous 5 years
  • Have an unresolved abnormal cancer screening test result before randomization
  • Have greater than trace amounts of glycosuria at screening, except for known diabetic patients
  • Have estimated creatinine clearance less than 50 mL/min
  • Have liver function tests (LFT) greater than 3 times the upper limit of normal (ULN)
  • Have any other clinically significant ECG or laboratory finding
  • Have any history of malignant melanoma
  • Have history of seizures (except febrile) or posttraumatic epilepsy
  • Have Mini-Mental State Exam (MMSE) score ≤ 26
  • Have taken another investigational drug within 60 days before the baseline visit
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (66)

Barrow Neurological Institute

Phoenix, Arizona, 85013, United States

Location

Mayo Clinic Arizona

Scottsdale, Arizona, 85259, United States

Location

University of Arkansas for Medical Services

Little Rock, Arkansas, 72205, United States

Location

The Parkinson's and Movement Disorders Institute

Fountain Valley, California, 92708, United States

Location

University of California Irvine

Irvine, California, 92697-4275, United States

Location

USC, Keck School of Pharmacy, Department of Neurology

Los Angeles, California, 90033-0046, United States

Location

California Medical Clinic for Movement Disorders

Oxnard, California, 93030, United States

Location

Department of Neurology - UC Davis Medical Center

Sacramento, California, 95817, United States

Location

University of California San Diego

San Diego, California, 92161, United States

Location

Stanford University Medical Center, Dept. of Neurology

Stanford, California, 94305, United States

Location

The Parkinson's Institute

Sunnyvale, California, 94089, United States

Location

University of Colorado Health Sciences Center

Denver, Colorado, 80262, United States

Location

Colorado Neurological Institute/Movement Disorders Center

Englewood, Colorado, 80110, United States

Location

University of Connecticut Health Center

Farmington, Connecticut, 06030, United States

Location

Institute for Neurodegenerative Disorders

New Haven, Connecticut, 06510, United States

Location

Davis Building - Neurology 8-B

Jacksonville, Florida, 32224, United States

Location

University of South Florida, Harbourside Medical Tower

Tampa, Florida, 33606, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Medical College of Georgia

Augusta, Georgia, 30912, United States

Location

Northwestern University, Department of Neurology

Chicago, Illinois, 60611, United States

Location

Rush-Presbyterian-St. Luke's Medical Center

Chicago, Illinois, 60612, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Indiana University of Medicine/Outpatient Clinical Research Facility

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Hospitals and Clinics, Department of Neurology

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center/Dept. of Neurology

Kansas City, Kansas, 66160, United States

Location

LSUHSC in Shreveport

Shreveport, Louisiana, 71130, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins University, Department of Neurology

Baltimore, Maryland, 21287, United States

Location

Center for Aging, Genetics and Neurodegeneration, Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Brigham and Womens Hospital/Neurology

Boston, Massachusetts, 02115, United States

Location

Boston University Medical Center, Department of Neurology

Boston, Massachusetts, 02118, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Clinical Neuroscience Center

Southfield, Michigan, 48034, United States

Location

University of Minnesota, Department of Neurology

Minneapolis, Minnesota, 55455, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

Creighton University/Department of Neurology

Omaha, Nebraska, 68131, United States

Location

UMDNJ Robert Wood Johnson Medical Center

New Brunswick, New Jersey, 08901, United States

Location

University of Medicine and Dentistry of New Jersey/Center for Aging

Stratford, New Jersey, 08084, United States

Location

Parkinson's Disease & Movement Disorders Center of AMC

Albany, New York, 12205, United States

Location

Movement Disorders Center/North Shore - LIJ Health System

Manhasset, New York, 11030, United States

Location

Long Island Jewish Medical Center

New Hyde Park, New York, 11040, United States

Location

Beth Israel Medical Center, Department of Neurology

New York, New York, 10003, United States

Location

Columbia Presbyterian Medical Center, Neurological Institute

New York, New York, 10032, United States

Location

University of Rochester, Department of Neurology

Rochester, New York, 14642, United States

Location

Duke University Medical Center

Durham, North Carolina, 27705, United States

Location

University of Cincinnati

Cincinnati, Ohio, 45267-0525, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Medical College of Ohio, Department of Neurology

Toledo, Ohio, 43614, United States

Location

Oregon Health Sciences University/Dept. of Neurology

Portland, Oregon, 97201-3098, United States

Location

Pennsylvania Hospital/Dept. of Neurology

Philadelphia, Pennsylvania, 19107, United States

Location

Brown University/Memorial Hospital of Rhode Island/Neurology Dept.

Pawtucket, Rhode Island, 02860, United States

Location

University of Tennessee Memphis, Semmes Murphy Clinic

Memphis, Tennessee, 38104, United States

Location

Parkinson's Disease Center and Movement Disorders Clinic/Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Scott and White Clinic/Texas A & M University

Temple, Texas, 76508, United States

Location

University of Virginia Health System/Adult Neurology

Charlottesville, Virginia, 22903, United States

Location

Medical College of Wisconsin, Department Neurology

Milwaukee, Wisconsin, 53226, United States

Location

University of Calgary

Calgary, Alberta, T2N 2N1, Canada

Location

University of Alberta - Glenrose Rehab Hospital

Edmonton, Alberta, T5G 0B7, Canada

Location

London Health Sciences Center - University Campus

London, Ontario, N6A 5A5, Canada

Location

Ottawa Hospital, Civic Site

Ottawa, Ontario, K1Y 4E9, Canada

Location

Toronto Hospital Western Division

Toronto, Ontario, M5T 2S8, Canada

Location

University of Sherbrooke

Fleurimont, Quebec, J1H 5N4, Canada

Location

Centre Hospitalier De L'Universite Montreal

Montreal, Quebec, H2W 1T8, Canada

Location

McGill Center for Studies in Aging

Verdun, Quebec, H4H 1R3, Canada

Location

Saskatoon District Health Board - Royal University Hospital

Saskatoon, Saskatchewan, S7N 0W8, Canada

Location

University of Puerto Rico, Clinical Research Center

San Juan, 00901, Puerto Rico

Location

Related Publications (2)

  • Schwarzschild MA, Schwid SR, Marek K, Watts A, Lang AE, Oakes D, Shoulson I, Ascherio A; Parkinson Study Group PRECEPT Investigators; Hyson C, Gorbold E, Rudolph A, Kieburtz K, Fahn S, Gauger L, Goetz C, Seibyl J, Forrest M, Ondrasik J. Serum urate as a predictor of clinical and radiographic progression in Parkinson disease. Arch Neurol. 2008 Jun;65(6):716-23. doi: 10.1001/archneur.2008.65.6.nct70003. Epub 2008 Apr 14.

  • Parkinson Study Group PRECEPT Investigators. Mixed lineage kinase inhibitor CEP-1347 fails to delay disability in early Parkinson disease. Neurology. 2007 Oct 9;69(15):1480-90. doi: 10.1212/01.wnl.0000277648.63931.c0. Epub 2007 Sep 19.

Related Links

MeSH Terms

Conditions

Parkinson Disease

Interventions

3,9-bis((ethylthio)methyl)-K-252a

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 26, 2002

First Posted

June 27, 2002

Study Start

March 1, 2002

Primary Completion

August 1, 2005

Study Completion

August 1, 2005

Last Updated

May 10, 2012

Record last verified: 2012-05

Locations