Vaincre la Mucoviscidose
22
4
4
13
Key Highlights
Risk & Performance
Pipeline Risk Assessment
Pipeline Risk Assessment
Based on historical performance
High Risk
Score: 60/100
13.6%
3 terminated/withdrawn out of 22 trials
81.3%
-5.3% vs industry average
14%
3 trials in Phase 3/4
0%
0 of 13 completed trials have results
Key Signals
Enrollment Performance
Analytics
Activity Timeline
Global Presence
Clinical Trials (22)
Prevalence of Exercise-induced Ventilatory Limitation and Associated Factors in Patients With Cystic Fibrosis Receiving Elexacaftor-Tezacaftor-Ivacaftor
Role: collaborator
Ivacaftor in French Patients With Cystic Fibrosis and a G551D Mutation
Role: collaborator
Prevalence and Impact of Depression and Anxiety in Cystic Fibrosis
Role: collaborator
Study of Circulating Blood Cell Monocytes as Predictive Biomarker of Bone Cystic Fibrosis Disease. Impact of CFTR Correctors.
Role: collaborator
Comparison of Non-invasive Measurement Methods of Hepatic Fibrosis in Cystic Fibrosis
Role: collaborator
Human Papillomavirus and Cervical Dysplasia in Women With Cystic Fibrosis
Role: collaborator
Oral Health Status of Cystic Fibrosis Patients. An Online Survey in Collaboration With the Vaincre la Mucoviscidose Patient Association.
Role: collaborator
Surrogate Markers of Response to New Therapies in Cystic Fibrosis Patients
Role: collaborator
Prospective Study of the Phenotypic Expression of Cystic Fibrosis (CF) Screened Positive Newborns With an Atypical Form of CF (DPAM)
Role: collaborator
Combating Diagnostic Wandering and Impasse for Cystic Fibrosis
Role: collaborator
T-lymphocytes CD8+/HLA-DR+ and Acute Rejection After Lung Transplantation
Role: collaborator
Epidemiology of Anaerobic Bacteria in Cystic Fibrosis Patients: Descriptive and Non-interventional Study
Role: collaborator
Urinary and Anorectal Functional Disorders and Their Impact on CF Adults (PerineoMucoRMO)
Role: collaborator
Correction of Nonsense Mutations in Cystic Fibrosis
Role: collaborator
Evaluation of the Lung Clearance Index
Role: collaborator
Quantitative Computed Tomodensitometry in Patients With Cystic Fibrosis
Role: collaborator
DNA Methylation and Lung Disease in Cystic Fibrosis
Role: collaborator
Oxygen Therapy in Cystic Fibrosis
Role: collaborator
Osteopathic Treatment in Adult Patients With Cystic Fibrosis
Role: collaborator
Cystic Fibrosis and Totally Implantable Vascular Access Devices
Role: collaborator