Other
Tuberous Sclerosis Alliance
Total Trials
5
Recruiting
0
Active
1
Completed
4
Success Rate
100.0%+13% vs avg
Key Highlights
Risk & Performance
Pipeline Risk Assessment
Pipeline Risk Assessment
Based on historical performance
Moderate Risk
Score: 35/100
Failure Rate
0.0%
0 terminated/withdrawn out of 5 trials
Success Rate
100.0%
+13.5% vs industry average
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
50%
2 of 4 completed trials have results
Key Signals
2 with results
Enrollment Performance
Analytics
Phase 2
3(100.0%)
3Total
Phase 2(3)
Activity Timeline
Global Presence
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Clinical Trials (5)
Showing 5 of 5 trials
NCT02461459Active Not Recruiting
Autism Spectrum Disorder (ASD) and Intellectual Disability (ID) Determinants in Tuberous Sclerosis Complex (TSC)
Role: collaborator
NCT00126672Phase 2Completed
RAPAMYCIN FOR KIDNEY ANGIOMYOLIPOMAS
Role: collaborator
NCT01780441Completed
Early Biomarkers of Autism in Infants With Tuberous Sclerosis Complex (TSC)
Role: collaborator
NCT01289912Phase 2Completed
Trial of RAD001 and Neurocognition in Tuberous Sclerosis Complex (TSC)
Role: collaborator
NCT00457808Phase 2Completed
Rapamycin Therapy for Patients With Tuberous Sclerosis Complex and Sporadic LAM
Role: collaborator
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