Key Highlights

Risk & Performance

Pipeline Risk Assessment

Pipeline Risk Assessment

Based on historical performance

Moderate Risk

Score: 45/100

Failure Rate

0.0%

0 terminated/withdrawn out of 3 trials

Success Rate

100.0%

+13.4% vs industry average

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 1 completed trials have results

Key Signals

1 recruiting

Enrollment Performance

Analytics

No phase data available

Activity Timeline

Global Presence

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Clinical Trials (3)

Showing 3 of 3 trials
NCT07712003Not Yet Recruiting

Natural History to Assess Disease in Patients With MPS IIIC

Role: lead

NCT05825131Recruiting

Natural History Study of Participants With Sanfilippo Syndrome Type IIIC

Role: lead

NCT05648851Completed

A Natural History Study of Sanfilippo Syndrome Type D

Role: lead

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