Cystic Fibrosis Trust
15
2
3
10
Key Highlights
Risk & Performance
Pipeline Risk Assessment
Pipeline Risk Assessment
Based on historical performance
Moderate Risk
Score: 45/100
6.7%
1 terminated/withdrawn out of 15 trials
90.9%
+4.4% vs industry average
7%
1 trials in Phase 3/4
20%
2 of 10 completed trials have results
Key Signals
Enrollment Performance
Analytics
Activity Timeline
Global Presence
Clinical Trials (15)
A Study of Females With CF Throughout Pregnancy and Post-partum, and Follow up of Their Offspring
Role: collaborator
Analysis of Remote Monitoring/Virtual Clinic Data in Adult Patients With Cystic Fibrosis (Project Breathe)
Role: collaborator
ANNE Sensor Monitoring in Cystic Fibrosis
Role: collaborator
ActivOnline: Physical Activity in Cystic Fibrosis Trial UK
Role: collaborator
A Study of RPL554 in Patients With Cystic Fibrosis
Role: collaborator
Perceptions of the CF Screening Protocol Incorporating NGS
Role: collaborator
Pilot Trial of ExACT (Exercise as Airway Clearance Therapy) for People With Cystic Fibrosis
Role: collaborator
Evaluation of Patient Access to People With Cystic Fibrosis (CF) and Healthcare Professionals
Role: collaborator
Understanding Gut Symptoms in People With Cystic Fibrosis
Role: collaborator
Gut Imaging for Function & Transit in Cystic Fibrosis Study 2
Role: collaborator
Home Monitoring to Predict Exacerbation in Cystic Fibrosis
Role: collaborator
Single Dose of pGM169/GL67A in CF Patients
Role: collaborator
First Study of Oral Cysteamine in Cystic Fibrosis
Role: collaborator
The Effects of Long Term Inhalation of Hypertonic Saline in Subjects With Cystic Fibrosis
Role: collaborator
Cystic Fibrosis Withdrawal of Inhaled Steroids Evaluation Study (CF WISE Study)
Role: collaborator
All 15 trials loaded