Principal Investigator
Paul Gissen, MD PhD
Great Ormond Street Hospital, London United Kingdom, WC1N 3JH
Total Trials
1
As PI
1
Completed
0
h-index
N/A
Publications
0
Years Active
0
Research Impact
h-index
N/A
Research impact score
Publications
0
Total publications
Trial Results
0
Published trial results
Citations
0
Total citations
Drug Portfolio
DRUG(1)
1 unique interventions1 categories
Analytics
Trial Phases
Phase 31
Trial Status
Other1
Role Distribution
Principal Investigator1
PI Rate100%
Activity Timeline
Clinical Trials (1)
Research Network
Collaboration Network
3 collaborators·3 connections
Network Legend
KOL
Current InvestigatorCO
High-influence CollaboratorCO
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Research Areas & Affiliations
Therapeutic Areas
Affiliations
Great Ormond Street Hospital, London United Kingdom, WC1N 3JH
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Clinical Trials (1)
Showing 1 of 1 trials
Study With Batten-1 (Miglustat Liquid Formulation) to Treat Ceroid Lipofuscinosis Neuronal 3 (CLN3) Disease
CLN3
All 1 trials loaded