Research Impact

h-index

N/A

Research impact score

Publications

0

Total publications

Trial Results

0

Published trial results

Citations

0

Total citations

Drug Portfolio

DRUG(1)
1 unique interventions1 categories

Analytics

Trial Phases

Phase 31

Trial Status

Completed1

Role Distribution

Principal Investigator1
PI Rate100%

Activity Timeline

Research Network

Collaboration Network

4 collaborators·6 connections
Network Legend
KOL
Current Investigator
CO
High-influence Collaborator
CO
Collaborator
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Research Areas & Affiliations

Affiliations

Nicklaus Children's Hospital f/k/a Miami Children's Hospital

Similar Key Opinion Leaders

Discover other key opinion leaders with similar research profiles, therapeutic areas, and collaboration networks.

10 similar investigators found

Chester Whitley, MD

University of Minnesota

Moderately Similar
1 trials

Shared therapeutic areas:

MPS 7MPS VIIMucopolysaccharidoses+1 more

Worked with same sponsors:

Ultragenyx Pharmaceutical Inc
Collaborated on 1 trial
Similarity Score44%

Raymond Wang, MD

Children's Hospital of Orange County

Moderately Similar
1 trials

Shared therapeutic areas:

MPS 7MPS VIIMucopolysaccharidoses+1 more

Worked with same sponsors:

Ultragenyx Pharmaceutical Inc
Collaborated on 1 trial
Similarity Score44%

Paul Harmatz, MD

UCSF Benioff Children's Hospital Oakland

Moderately Similar
2 trials

Shared therapeutic areas:

MPS 7MPS VIIMucopolysaccharidoses+1 more

Worked with same sponsors:

Ultragenyx Pharmaceutical Inc
Collaborated on 1 trial
Similarity Score44%

Paul Orchard, MD

Masonic Cancer Center, University of Minnesota

Related
9 trials

Shared therapeutic areas:

MucopolysaccharidosesMucopolysaccharidosis VII
Similarity Score15%

Chester B. Whitley, M.D., Ph.D.

University of Minnesota

Related
1 trials

Shared therapeutic areas:

Mucopolysaccharidosis VII
Similarity Score8%

James Hinson, MD

Aldagen

Related
1 trials

Shared therapeutic areas:

Mucopolysaccharidoses
Similarity Score8%

Aaron S Kelly, Ph.D.

University of Minnesota

Related
4 trials

Shared therapeutic areas:

Mucopolysaccharidoses
Similarity Score8%

Tippi C MacKenzie, MD

University of California, San Francisco

Related
2 trials

Shared therapeutic areas:

Mucopolysaccharidosis VII
Similarity Score8%

Lynda E Polgreen, MD, MS

Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center

Related
2 trials

Shared therapeutic areas:

Mucopolysaccharidoses
Similarity Score8%

Naciye Vardar- Yagli, PhD

Hacettepe University

Related
1 trials

Shared therapeutic areas:

Mucopolysaccharidoses
Similarity Score8%

Publications (0)

No publications found for this investigator.

Clinical Trials (1)

Showing 1 of 1 trials

NCT02230566Phase 3PrincipalInvestigator

A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7)

MPS 7MPS VIIMucopolysaccharidosis+1 more
Completed

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