Success Metrics

Clinical Success Rate
100.0%

Based on 14 completed trials

Completion Rate
100%(14/14)
Active Trials
3(11%)
Results Posted
43%(6 trials)

Phase Distribution

Ph phase_1
5
19%
Ph phase_2
14
52%
Ph early_phase_1
2
7%
Ph phase_3
1
4%

Phase Distribution

7

Early Stage

14

Mid Stage

1

Late Stage

Phase Distribution22 total trials
Early Phase 1First-in-human
2(9.1%)
Phase 1Safety & dosage
5(22.7%)
Phase 2Efficacy & side effects
14(63.6%)
Phase 3Large-scale testing
1(4.5%)

Highest Phase Reached

Phase 3

Trial Status & Enrollment

Completion Rate

93.3%

14 of 15 finished

Non-Completion Rate

6.7%

1 ended early

Currently Active

3

trials recruiting

Total Trials

27

all time

Status Distribution
Active(3)
Completed(14)
Terminated(1)
Other(9)

Detailed Status

Completed14
unknown8
Recruiting2
Withdrawn1
Active, not recruiting1
Suspended1

Development Timeline

Analytics

Development Status

Total Trials
27
Active
3
Success Rate
100.0%
Most Advanced
Phase 3

Trials by Phase

Early Phase 12 (9.1%)
Phase 15 (22.7%)
Phase 214 (63.6%)
Phase 31 (4.5%)

Trials by Status

completed1452%
withdrawn14%
active_not_recruiting14%
recruiting27%
suspended14%
unknown830%

Recent Activity

Clinical Trials (27)

Showing 20 of 27 trialsScroll for more
NCT06067802Phase 2

Study of Triheptanoin for the Prevention of Hypoglycemia in Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)

Suspended
NCT03773770

Expanded Access to Triheptanoin

Unknown
NCT07097311Phase 2

Study to Evaluate the Use of Triheptanoin in Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)

Recruiting
NCT06340685Phase 1

Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency

Recruiting
NCT05933200Phase 3

A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD

Active Not Recruiting
NCT02408354Phase 2

Pilot Study, Comparative, Single-center, Randomized, Crossover, Double-blind, Against Placebo, Testing the Effectiveness of Triheptanoin Oil in Alternating Hemiplegia of Childhood

Completed
NCT02919631Phase 2

Triheptanoin in Mc Ardle

Completed
NCT03181399Phase 2

Diet Treatment Glucose Transporter Type 1 Deficiency (G1D)

Completed
NCT03642860Phase 2

The Effect of Triheptanoin on Fatty Acid Oxidation and Exercise Tolerance in Patients With Glycogenoses

Completed
NCT03301532Phase 2

Compatibility of C7 With Ketogenic Diet in Patients Diagnosed With G1D

Completed
NCT04513002Phase 2

Ataxia-telangiectasia: Treating Mitochondrial Dysfunction With a Novel Form of Anaplerosis

Completed
NCT03041363Phase 1

Treatment Development of Triheptanoin (G1D)

Completed
NCT03665636Early Phase 1

Anaplerotic Therapy Using Triheptanoin for Patients With Glycogen Storage Disease Type I

Completed
NCT01461304

Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism

Unknown
NCT02036853Phase 2

An Open-Label Trial of Triheptanoin in Patients With Glucose Transporter Type-1 Deficiency Syndrome

Completed
NCT02696044Phase 2

Treatment of Mitochondrial Dysfunction in Rett Syndrome With Triheptanoin

Unknown
NCT03506425Phase 1

A Pilot Trial of Triheptanoin for People With Amyotrophic Lateral Sclerosis (PALS)

Completed
NCT02018315Phase 1

Treatment Development for Glucose Transporter Type I Deficiency Syndrome (G1D)

Completed
NCT02432768Phase 2

The Effect of Triheptanoin in Adults With McArdle Disease (Glycogen Storage Disease Type V)

Completed
NCT02018302

Post Study Continuation of C7 for G1D

Unknown

Drug Details

Intervention Type
DRUG
Total Trials
27