X-Linked Myotubular Myopathy
7
3
4
3
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 7 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
33%
1 of 3 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 3 completed trials
Clinical Trials (7)
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
Myotubular and Centronuclear Myopathy Patient Registry
A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects
Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM)
Myotubular Myopathy Event Study