Wolfram Syndrome
11
3
4
4
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 11 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
25%
1 of 4 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 4 completed trials
Clinical Trials (11)
Efficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome
AMX0035 in Adult Patients With Wolfram Syndrome
Mechanisms of Fecal Incontinence in Wolfram Syndrome
Wolfram Syndrome and WFS1-related Disorders International Registry and Clinical Study
Monogenic Diabetes Misdiagnosed as Type 1
I-Tracking Neurodegeneration in Early Wolfram Syndrome
A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome
Tirzepatide Monotherapy in Patients With Wolfram Syndrome Type 1
Efficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome
GLP Analogs for Diabetes in Wolfram Syndrome Patients
Tracking Neurodegeneration in Early Wolfram Syndrome