Condition
Trifunctional Protein Deficiency
Total Trials
4
Recruiting
0
Active
0
Completed
4
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 25/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
75%
3 of 4 completed with results
Key Signals
3 with results100% success
Data Visualizations
Phase Distribution
3Total
Not Applicable (1)
Early P 1 (1)
P 1 (1)
Trial Status
Completed4
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 4 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT05411835Early Phase 1Completed
Oral Ketones and Exercise Among Patients With Long-chain Fatty Acid Oxidation Disorders
NCT02517307Not ApplicableCompleted
Fatty Acid Oxidation Defects and Insulin Sensitivity
NCT01494051Phase 1Completed
High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders
NCT00654004CompletedPrimary
Fatty Acid Oxidation Disorders & Body Weight Regulation Grant
Showing all 4 trials