Key Insights

Highlights

Success Rate

100% trial completion (above average)

Related Conditions

Often studied with 10 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 1 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

Trial Status

Completed1
Not Yet Recruiting1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (2)

Research Network

Active Sponsors

  • Duke University1
  • University Hospital, Grenoble1

Top Investigators

Related Conditions

  • Glycogen Storage Disease1
  • Lysosomal Storage Diseases1
  • Malformation1
  • Genetic Disease1
  • Neuromuscular Disease1

Activity Timeline