Key Insights

Highlights

Success Rate

100% trial completion (above average)

Research Leaders

5 sponsors active, led by Institut National de la Santé Et de la Recherche Médicale, France

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 2 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

Trial Status

Completed2

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 2 completed trials

Clinical Trials (2)

Research Network

Active Sponsors

  • Institut National de la Santé Et de la Recherche Médicale, France2
  • Assistance Publique - Hôpitaux de Paris1
  • National Research Agency, France1
  • Paris Brain Institute (ICM)1
  • Institut des Maladies Rares1

Top Investigators

Related Conditions

  • Cerebellar Ataxias1
  • Spinocerebellar Ataxias1

Activity Timeline