Condition
SMA - Spinal Muscular Atrophy
Total Trials
5
Recruiting
2
Active
3
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 5/100
Termination Rate
0.0%
0 terminated out of 5 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
40%
2 trials in Phase 3/4
Results Transparency
100%
1 of 1 completed with results
Key Signals
1 with results100% success
Data Visualizations
Phase Distribution
3Total
Not Applicable (1)
P 3 (2)
Trial Status
Recruiting2
Not Yet Recruiting1
Active Not Recruiting1
Completed1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (5)
Showing 5 of 5 trials
NCT07530926Not Yet RecruitingPrimary
Adrenal& Bone Complications in Paediatric Patients Living With Spinal Muscular Atrophy (SMA)
NCT07467187Recruiting
Invasive Home Ventilation in Denmark
NCT07223320Not ApplicableActive Not RecruitingPrimary
HABIT-ILE + FST in Children With SMA
NCT03306277Phase 3CompletedPrimary
Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
NCT06971094Phase 3RecruitingPrimary
Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Showing all 5 trials