Primary Hyperoxaluria
23
4
4
16
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 40/100
0.0%
0 terminated out of 23 trials
100.0%
+13.5% vs benchmark
13%
3 trials in Phase 3/4
38%
6 of 16 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 16 completed trials
Clinical Trials (23)
Nedosiran in Pediatric Patients From Birth to 11 Years of Age With PH and Relatively Intact Renal Function
Baby Detect : Genomic Newborn Screening
Rare Kidney Stone Consortium Biobank
A Study to Evaluate Lumasiran in Patients With Advanced Primary Hyperoxaluria Type 1
Rare Kidney Stone Consortium Patient Registry
A Study of Lumasiran in Infants and Young Children With Primary Hyperoxaluria Type 1
Study of DCR-PHXC-101 in Normal Healthy Volunteers and Patients With Primary Hyperoxaluria
An Extension Study of an Investigational Drug, Lumasiran (ALN-GO1), in Participants With Primary Hyperoxaluria Type 1
Expanded Access Protocol to Provide Lumasiran to Patients With Primary Hyperoxaluria Type 1
National Registry of Rare Kidney Diseases
Genetic Newborn Screening for Cystinosis and Primary Hyperoxaluria
Health-related Quality of Life in Rare Kidney Stone
Study to Evaluate the Efficacy and Safety of Oxabact (OC5) in Primary Hyperoxaluria Patients Who Are on Dialysis
A Study to Evaluate the Efficacy and Safety of Oxabact in Patients With Primary Hyperoxaluria
Phenotyping of Primary Hyperoxaluria
Evaluation of the Efficacy of Stiripentol (Diacomit) as Monotherapy for the Treatment of Primary Hyperoxaluria
Study of ALLN-177 in Patients Aged 12 Years or Older With Enteric or Primary Hyperoxaluria and Hyperoxalemia
Primary Hyperoxaluria Mutation Genotyping/Phenotyping
Primary Hyperoxaluria Mutation Genotyping
Study to Evaluate the Efficacy and Safety of Oxabact (OC5) in Patients With Primary Hyperoxaluria