Primary Ciliary Dyskinesia
59
12
14
31
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 59 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
10%
3 of 31 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 31 completed trials
Clinical Trials (59)
A Longitudinal, Observational Study of Primary Ciliary Dyskinesia in Adults
Genetic Disorders of Mucociliary Clearance in Nontuberculous Mycobacterial Lung Disease
A Cohort for Inflammatory Respiratory Diseases: From Phenotyping to Personalised Medicine
DCP (RaDiCo Cohort) (RaDiCo-DCP)
Examining Bronchial Hyperresponsiveness in Primary Ciliary Dyskinesia
Longitudinal Characterization of Respiratory Tract Exacerbations and Treatment Responses in Primary Ciliary Dyskinesia
The Ear-Nose-Throat (ENT) Prospective International Cohort of PCD Patients (EPIC-PCD)
Living With Primary Ciliary Dyskinesia (Living With PCD)
International Primary Ciliary Dyskinesia Cohort
Glycine and Magnesium+Thiamine for the Treatment of Primary Ciliary Dyskinesia
Swiss Primary Ciliary Dyskinesia Registry
A Study to Assess the Safety, Tolerability, Ciliary Rescue, and Pharmacodynamics of RCT1100 in Adults With PCD
Utility of PCD Diagnostics to Improve Clinical Care
Functional Studies of Novel Genes Mutated in Primary Ciliary Dyskinesia II: Genotype to Phenotype
Defining the Genetic Etiology of Suppurative Lung Disease in Children and Adults
Characterizing the Upper Airway Manifestations in Primary Ciliary Dyskinesia and Primary Immunodeficiencies
Utility of PCD Diagnostics to Improve Clinical Care
Thermal Spa Treatment and Improvement of Primary Ciliary Dyskinesia
A Study Providing Genetic Testing to Find Those Who May Have Primary Ciliary Dyskinesia for Potential Clinical Trials
Study Evaluating the Safety and Tolerability of RCT1100 in Healthy and PCD Subjects