Key Insights

Highlights

Success Rate

93% trial completion (above average)

Published Results

14 trials with published results (19%)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 30/100

Termination Rate

4.1%

3 terminated out of 73 trials

Success Rate

93.3%

+6.8% vs benchmark

Late-Stage Pipeline

26%

19 trials in Phase 3/4

Results Transparency

33%

14 of 42 completed with results

Key Signals

14 with results93% success

Data Visualizations

Phase Distribution

57Total
Not Applicable (8)
Early P 1 (1)
P 1 (11)
P 2 (18)
P 3 (14)
P 4 (5)

Trial Status

Completed42
Unknown14
Recruiting5
Withdrawn5
Active Not Recruiting3
Terminated3

Trial Success Rate

93.3%

Benchmark: 86.5%

Based on 42 completed trials

Clinical Trials (73)

Showing 20 of 20 trials
NCT03301506Phase 3Active Not RecruitingPrimary

Study of Seladelpar in Participants With Primary Biliary Cholangitis (PBC)

NCT04526665Phase 3Active Not RecruitingPrimary

Study of Elafibranor in Patients With Primary Biliary Cholangitis (PBC)

NCT06519162Recruiting

Liver-gut Axis Study Through Identification of Liver Disease-specific Microbiome

NCT03445585Recruiting

Biobank for Cholestatic Liver Diseases.

NCT03743272Completed

Repeatability and Reproducibility of Multiparametric MRI

NCT01161953CompletedPrimary

Genetic Epidemiology of Primary Biliary Cirrhosis (PBC)

NCT06061341Enrolling By Invitation

TruGraf Liver Gene Expression Serial Test

NCT02846896CompletedPrimary

The Health Burden of Primary Biliary Cirrhosis (PBC) in Switzerland

NCT01793168Recruiting

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

NCT01614405Not ApplicableTerminatedPrimary

Highly Active Antiretroviral Therapy for Patients With Primary Biliary Cirrhosis

NCT03112681Phase 2CompletedPrimary

Study to Evaluate Safety, Tolerability and Efficacy of Saroglitazar Mg in Patients With Primary Biliary Cholangitis

NCT04522869Phase 1CompletedPrimary

Umbilical Cord Derived Mesenchymal Stem Cell (UC -MSC) Transplantation for Children Suffering From Biliary Atresia

NCT04604652Phase 2Completed

Open-Label Study of HTD1801 in Adult Subjects With Primary Biliary Cholangitis

NCT02963077Phase 1Completed

A Safety and Pharmakokinetic Study of A4250 Alone or in Combination With A3384

NCT03082937Phase 1Completed

An Open Label, Single-dose, Single Period ADME Study of A4250 in Healthy Subjects

NCT04791527Not ApplicableCompletedPrimary

Online Wellness Intervention for Primary Biliary Cholangitis (PBC)

NCT02823353Phase 3CompletedPrimary

Fenofibrate in Combination With Ursodeoxycholic Acid in Primary Biliary Cirrhosis

NCT02823366Phase 3UnknownPrimary

Fenofibrate for Patients With Primary Biliary Cirrhosis Who Had An Inadequate Response to Ursodeoxycholic Acid

NCT01865812Phase 2CompletedPrimary

Phase 2 Study on Effects of Obeticholic Acid (OCA) on Lipoprotein Metabolism in Participants With Primary Biliary Cirrhosis

NCT02924701Active Not RecruitingPrimary

sCD163 in PBC Patients - Assessment of Disease Severity and Prognosis

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Research Network

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