Key Insights

Highlights

Related Conditions

Often studied with 6 related conditions

Clinical Risk Assessment

Based on trial outcomes

High Risk

Score: 100/100

Termination Rate

100.0%

1 terminated out of 1 trials

Success Rate

0.0%

-86.6% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

0

Data Visualizations

Phase Distribution

Trial Status

Terminated1

Clinical Trials (1)

Research Network

Active Sponsors

  • Alnylam Pharmaceuticals1

Top Investigators

Related Conditions

  • Ala Dehydratase Deficient Porphyria Adp1
  • Variegate Porphyria Vp1
  • Hereditary Coproporphyria Hcp1
  • Acute Hepatic Porphyria1
  • Acute Intermittent Porphyria Aip1

Activity Timeline