Organic Acidemia
5
3
3
1
Key Insights
Highlights
Success Rate
50% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 85/100
20.0%
1 terminated out of 5 trials
50.0%
-36.5% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 1 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (5)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
Clinical and Laboratory Study of Methylmalonic Acidemia
Systemic Biomarkers of Brain Injury From Hyperammonemia
A First in Human, Dose Escalation Study to Evaluate the Safety and Tolerability of BBP-671 in Healthy Volunteers and Patients With Propionic Acidemia or Methylmalonic Acidemia
The Effect of the Cognitive Orientation to Daily Occupational Performance Approach for Children With Organic Acidemia