Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

1 treatments under study, led by 15 O Water

Research Leaders

20 sponsors active, led by National Institute of Neurological Disorders and Stroke (NINDS)

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0 trials in Phase 3/4

Results Transparency

0 of 1 completed with results

Key Signals

100% success

Data Visualizations

Phase Distribution

Trial Status

Recruiting1

Completed1

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (2)

Showing 2 of 2 trials

NCT06985212Recruiting

National Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and Children

NCT00001972Completed

PET Scan of Brain Metabolism in Relation to Age and Disease

Showing all 2 trials

Research Network

Common Treatments

15 O Water1

Active Sponsors

National Institute of Neurological Disorders and Stroke (NINDS)1
Centre Hospitalier Saint Joseph Saint Luc de Lyon1
Centre Hospitalier de Cornouaille1
Hospices Civils de Lyon1
Centre Hospitalier Universitaire de Saint Etienne1

Niemann Pick Disease