Key Insights

Highlights

Treatment Research

1 treatments under study, led by Ngn101

Related Conditions

Often studied with 9 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 2 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

1Total
Phase 1/2 (1)

Trial Status

Recruiting1
Active Not Recruiting1

Clinical Trials (2)

Research Network

Common Treatments

  • Ngn1011

Active Sponsors

  • Neurogene Inc.1
  • University of Rochester1

Top Investigators

Related Conditions

  • Neuronal Ceroid Lipofuscinosis Cln71
  • Neuronal Ceroid Lipofuscinosis Cln61
  • Neuronal Ceroid Lipofuscinosis Cln81
  • Batten Disease1
  • Neuronal Ceroid Lipofuscinosis Cln31

Activity Timeline