Condition
Neurogenetic Disorders
Total Trials
4
Recruiting
3
Active
3
Completed
0
Key Insights
Highlights
No notable highlights available yet
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 4 trials
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
Data Visualizations
Phase Distribution
2Total
Not Applicable (1)
P 1 (1)
Trial Status
Recruiting3
Not Yet Recruiting1
Clinical Trials (4)
Showing 4 of 4 trials
NCT07695610Recruiting
Pediatric Movement Disorders of Unknown Etiology in Vietnam (VPeMD)
NCT02995538RecruitingPrimary
Neurogenetics Patient Registry
NCT06725901Not ApplicableRecruiting
Pediatric Neurogenetic Diagnosis Support Platform
NCT06948019Phase 1Not Yet Recruiting
Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)
Showing all 4 trials