Condition
Neurodegeneration With Brain Iron Accumulation (NBIA)
Total Trials
5
Recruiting
3
Active
3
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 5 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
1Total
Not Applicable (1)
Trial Status
Recruiting3
Completed1
Unknown1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (5)
Showing 5 of 5 trials
NCT05522374RecruitingPrimary
TIRCON International NBIA Registry
NCT06596746Recruiting
Neurodegenerative Diseases Progression Markers (MARKERS-NDD)
NCT05696912Not ApplicableRecruiting
Functional Tests to Resolve Unsolved Rare Diseases. Rares.
NCT05615571CompletedPrimary
Testing of NBIA Genes: Analysis of Genetic Heterogeneity and Validation of Mitochondrial Markers for Assessing Causality of Sequence Variants.
NCT02587858UnknownPrimary
NBIAready: Online Collection of Natural History Patient-reported Outcome Measures
Showing all 5 trials