Condition
Nephropathic Cystinosis
Total Trials
6
Recruiting
3
Active
3
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 25/100
Termination Rate
0.0%
0 terminated out of 6 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
100%
1 of 1 completed with results
Key Signals
1 with results100% success
Data Visualizations
Phase Distribution
2Total
Not Applicable (1)
P 1 (1)
Trial Status
Recruiting3
Enrolling By Invitation1
Completed1
Unknown1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (6)
Showing 6 of 6 trials
NCT06910813Phase 1RecruitingPrimary
DFT383 in Pediatric Participants With Nephropathic Cystinosis
NCT01793168Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT03919981RecruitingPrimary
CYSTEA-BONE Clinical Study
NCT04246060Enrolling By InvitationPrimary
Observational Study to Assess the Quality of Life in Nephropathic Cystinosis Patients
NCT01327807Unknown
Cure Cystinosis International Registry
NCT01432561Not ApplicableCompleted
Study in Healthy Adults to Determine the Effect That Food Has on the Absorption and Delivery of the Drug Cystagon™
Showing all 6 trials