Nemaline Myopathy
11
4
5
2
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 11 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
0%
0 of 2 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 2 completed trials
Clinical Trials (11)
Natural History Study for Patients With Nemaline Myopathy in the UK
Molecular and Genetic Studies of Congenital Myopathies
Natural History Study for Patients With Nemaline Myopathy in Belgium
Natural History Study for Patients With Nemaline Myopathy in Spain
Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Changes of Motor Function Tests in Congenital Myopathy Subjects Treated With Oral Salbutamol as Compared to no Treatment
The Prevalence of RYR1-related Disease
Nemaline Myopathy Clinical Research Network (NM-CTRN)
Inspiratory Muscle Training in Nemaline Myopathy
The Natural History and Muscle Fatigability of Patients With Congenital Myopathies.
Treatment of TNNT1-Myopathy With L-Tyrosine.