Condition
N-acetylglutamate Synthase Deficiency
Total Trials
3
Recruiting
0
Active
0
Completed
0
Key Insights
Highlights
No notable highlights available yet
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 100/100
Termination Rate
33.3%
1 terminated out of 3 trials
Success Rate
0.0%
-86.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
0
Data Visualizations
Phase Distribution
Trial Status
Unknown1
Enrolling By Invitation1
Terminated1
Clinical Trials (3)
Showing 3 of 3 trials
NCT03655223Enrolling By Invitation
Early Check: Expanded Screening in Newborns
NCT05910151Unknown
Selective Screening of Children for Hereditary Metabolic Diseases by Tandem Mass Spectrometry in Kazakhstan
NCT01421888Terminated
The NIH UNI Study: Urea Cycle Disorders, Nutrition and Immunity
Showing all 3 trials