Condition
Myotonia Congenita
Total Trials
5
Recruiting
0
Active
0
Completed
5
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 30/100
Termination Rate
0.0%
0 terminated out of 5 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
40%
2 trials in Phase 3/4
Results Transparency
0%
0 of 5 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
3Total
P 1 (1)
P 3 (2)
Trial Status
Completed5
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 5 completed trials
Clinical Trials (5)
Showing 5 of 5 trials
NCT04799366Completed
Contractile Properties of Hypertrofic Muscles in Patients With Non-Dystrophic Myotonia
NCT02251457Phase 1CompletedPrimary
Study of Ranolazine in Myotonia Congenita, Paramyotonia Congenita and Myotonic Dystrophy Type 1
NCT01939561Phase 3Completed
Lamotrigine as Treatment of Myotonia
NCT02336477Phase 3Completed
Mexiletine and Non Dystrophic Myotonias
NCT00244413Completed
Characteristics of Nondystrophic Myotonias
Showing all 5 trials