Key Insights

Highlights

Success Rate

100% trial completion (above average)

Treatment Research

2 treatments under study, led by Whole Exome Sequencing Wes

Related Conditions

Often studied with 9 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 37/100

Termination Rate

0.0%

0 terminated out of 2 trials

Success Rate

100.0%

+13.4% vs benchmark

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

50%

1 of 2 completed with results

Key Signals

1 with results100% success

Data Visualizations

Phase Distribution

2Total
Not Applicable (2)

Trial Status

Completed2

Trial Success Rate

100.0%

Benchmark: 86.6%

Based on 2 completed trials

Clinical Trials (2)

Research Network

Common Treatments

  • Whole Exome Sequencing Wes1
  • Face2gene1

Active Sponsors

  • Manchester University NHS Foundation Trust1
  • FDNA Inc.1
  • University of California, San Francisco1

Top Investigators

Related Conditions

  • Gastrointestinal Anomalies1
  • Genitourinary Anomalies1
  • Inborn Errors Of Metabolism1
  • Thorax Anomalies1
  • Skeletal Anomalies1

Activity Timeline