Condition
Mucolipidosis Type IV
Total Trials
4
Recruiting
0
Active
1
Completed
1
Success Rate
50.0%-37% vs avg
Key Insights
Highlights
Success Rate
50% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 100/100
Termination Rate
25.0%
1 terminated out of 4 trials
Success Rate
50.0%
-36.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
50% success
Data Visualizations
Phase Distribution
1Total
P 1 (1)
Trial Status
Enrolling By Invitation1
Terminated1
Completed1
Active Not Recruiting1
Trial Success Rate
50.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT05782387Active Not RecruitingPrimary
Mucolipidosis Type IV Natural History Study
NCT07398872Phase 1Enrolling By InvitationPrimary
Safety and Efficacy of AAV9. hMCOLN1co For Patients With Mucolipidosis Type IV
NCT01067742TerminatedPrimary
The Natural History of Mucolipidosis Type IV
NCT00015782CompletedPrimary
The Natural History and Pathogenesis of Mucolipidosis Type IV
Showing all 4 trials