Monocarboxylate Transporter 8 (MCT8) Deficiency
3
0
1
2
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Treatment Research
1 treatments under study, led by Tiratricol
Research Leaders
5 sponsors active, led by Rare Thyroid Therapeutics International AB
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 30/100
0.0%
0 terminated out of 3 trials
100.0%
+13.4% vs benchmark
33%
1 trials in Phase 3/4
0%
0 of 2 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.6%
Based on 2 completed trials
Clinical Trials (3)
Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)
Triac Trial II in MCT8 Deficiency Patients
MCT8 Deficiency Caregiver Study
Research Network
Common Treatments
- Tiratricol2
Active Sponsors
- Rare Thyroid Therapeutics International AB3
- Erasmus Medical Center1
- Premier Research1
- Vitaccess Ltd1
- Egetis Therapeutics AB (publ)1
Top Investigators
Charité - Universitätsmedizin Berlin Institut fur experimental paediatrische endokrinologie
Erasmus Medical Center
Oregon Health& Science University (OHSU) Doernbecher Childrens Hospital
Charles University and Motol University Hospital
Rare Thyroid Therapeutics International AB
Related Conditions
- Allanherndondudley Syndrome3
- Monocarboxylate Transporter 8 Deficiency1