Condition
Mitochondrial Trifunctional Protein Deficiency
Total Trials
3
Recruiting
0
Active
0
Completed
0
Key Insights
Highlights
No notable highlights available yet
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 100/100
Termination Rate
33.3%
1 terminated out of 3 trials
Success Rate
0.0%
-86.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
0
Data Visualizations
Phase Distribution
1Total
Not Applicable (1)
Trial Status
Terminated1
Enrolling By Invitation1
Unknown1
Clinical Trials (3)
Showing 3 of 3 trials
NCT03655223Enrolling By Invitation
Early Check: Expanded Screening in Newborns
NCT01461304Unknown
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
NCT00840112Not ApplicableTerminated
Vitamin E Treatment for Long-Chain 3-Hydroxyacyl Coenzyme A (CoA) Dehydrogenase (LCHAD) Associated Neuropathy
Showing all 3 trials