Condition
Lysosomal Storage Disorders
Total Trials
4
Recruiting
0
Active
0
Completed
0
Key Insights
Highlights
No notable highlights available yet
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 90/100
Termination Rate
25.0%
1 terminated out of 4 trials
Success Rate
0.0%
-86.5% vs benchmark
Late-Stage Pipeline
25%
1 trials in Phase 3/4
Results Transparency
0%
0 of 0 completed with results
Key Signals
0
Data Visualizations
Phase Distribution
1Total
P 3 (1)
Trial Status
Unknown2
Enrolling By Invitation1
Terminated1
Clinical Trials (4)
Showing 4 of 4 trials
NCT00001215Enrolling By InvitationPrimary
Genetic Studies of Lysosomal Storage Disorders
NCT02000310UnknownPrimary
Molecular and Cellular Mechanisms of Lysosomal Storage Diseases
NCT02120235UnknownPrimary
Investigating Lysosomal Storage Diseases in Minority Groups
NCT00654433Phase 3Terminated
ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
Showing all 4 trials