Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency
7
0
0
4
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 37/100
0.0%
0 terminated out of 7 trials
100.0%
+13.5% vs benchmark
0%
0 trials in Phase 3/4
50%
2 of 4 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Trial Success Rate
Benchmark: 86.5%
Based on 4 completed trials
Clinical Trials (7)
Baby Detect : Genomic Newborn Screening
Early Check: Expanded Screening in Newborns
Oral Ketones and Exercise Among Patients With Long-chain Fatty Acid Oxidation Disorders
Fatty Acid Oxidation Defects and Insulin Sensitivity
Selective Screening of Children for Hereditary Metabolic Diseases by Tandem Mass Spectrometry in Kazakhstan
High Protein Diet in Patients With Long-chain Fatty Acid Oxidation Disorders
Fat and Sugar Metabolism During Exercise in Patients With Metabolic Myopathy