Condition
Limb-Girdle Muscular Dystrophy, Type 2I (FKRP-deficiency)
Total Trials
1
Recruiting
0
Active
0
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 1 trials
Success Rate
100.0%
+13.4% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 1 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
Trial Status
Completed1
Trial Success Rate
100.0%
Benchmark: 86.6%
Based on 1 completed trials
Clinical Trials (1)
Showing 1 of 1 trials
Showing all 1 trials
Research Network
Active Sponsors
- Carolinas Medical Center lead study site1
- Cooperative International Neuromuscular Research Group1
Top Investigators
Levine Children's Hospital
Cooperative International Neuromuscular Research Group
Related Conditions
- Becker Muscular Dystrophy1
- Limbgirdle Muscular Dystrophy Type 2b Miyoshi Myopathy Dysferlin Deficiency1
- Limbgirdle Muscular Dystrophy Type 2a Calpain3 Deficiency1