Condition
LHON
Total Trials
4
Recruiting
1
Active
1
Completed
1
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Low Risk
Score: 25/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
100%
1 of 1 completed with results
Key Signals
1 with results100% success
Data Visualizations
Phase Distribution
1Total
P 1 (1)
Trial Status
Enrolling By Invitation2
Recruiting1
Completed1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 1 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT01803906Enrolling By Invitation
Tissue Sample Study for Mitochondrial Disorders
NCT05554835Recruiting
Global Registry and Natural History Study for Mitochondrial Disorders
NCT06376279Enrolling By Invitation
Genetic Diagnosis in Inborn Errors of Metabolism
NCT02544217Phase 1Completed
A Dose-escalating Clinical Trial With KH176
Showing all 4 trials