Condition
Leukodystrophy
Total Trials
7
Recruiting
5
Active
5
Completed
2
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 37/100
Termination Rate
0.0%
0 terminated out of 7 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
50%
1 of 2 completed with results
Key Signals
1 with results100% success
Data Visualizations
Phase Distribution
1Total
Not Applicable (1)
Trial Status
Recruiting5
Completed2
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 2 completed trials
Clinical Trials (7)
Showing 7 of 7 trials
NCT03333200Recruiting
Longitudinal Study of Neurodegenerative Disorders
NCT03639285RecruitingPrimary
Natural History, Diagnosis, and Outcomes for Leukodystrophies
NCT02699190CompletedPrimary
LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
NCT03047369RecruitingPrimary
The Myelin Disorders Biorepository Project
NCT01793168Recruiting
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT05443906Not ApplicableRecruiting
Home Exercise for Individuals with Neurodegenerative Disease
NCT00889174CompletedPrimary
The Nosology and Etiology of Leukodystrophies of Unknown Causes
Showing all 7 trials