Key Insights

Highlights

Research Leaders

6 sponsors active, led by National Institute of Neurological Disorders and Stroke (NINDS)

Related Conditions

Often studied with 4 related conditions

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 1 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

Trial Status

Recruiting1

Clinical Trials (1)

Showing 1 of 1 trials
Showing all 1 trials

Research Network

Active Sponsors

  • National Institute of Neurological Disorders and Stroke (NINDS)1
  • National Center for Advancing Translational Sciences (NCATS)1
  • University of Minnesota1
  • Rare Diseases Clinical Research Network1
  • National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)1

Top Investigators

Related Conditions

  • Gm1 Gangliosidosis1
  • Taysachs Disease1
  • Gm2 Gangliosidosis1
  • Sandhoff Disease1

Activity Timeline