Condition
Late Infantile Neuronal Ceroid Lipofuscinosis
Total Trials
4
Recruiting
0
Active
0
Completed
3
Success Rate
75.0%-12% vs avg
Key Insights
Highlights
Success Rate
75% trial completion
Clinical Risk Assessment
Based on trial outcomes
High Risk
Score: 87/100
Termination Rate
25.0%
1 terminated out of 4 trials
Success Rate
75.0%
-11.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 3 completed with results
Key Signals
75% success
Data Visualizations
Phase Distribution
2Total
P 1 (2)
Trial Status
Completed3
Terminated1
Trial Success Rate
75.0%
Benchmark: 86.5%
Based on 3 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT01414985Phase 1CompletedPrimary
AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis
NCT01035424Completed
Genotype-Phenotype Correlations of Late Infantile Neuronal Ceroid Lipofuscinosis
NCT00151216Phase 1Completed
Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis
NCT01698229TerminatedPrimary
Collection of Cerebrospinal Fluid in Healthy Children
Showing all 4 trials