Laminopathies
4
3
3
0
Key Insights
Highlights
Treatment Research
3 treatments under study, led by Skin Biopsy
Research Leaders
5 sponsors active, led by Institut National de la Santé Et de la Recherche Médicale, France
Related Conditions
Often studied with 20 related conditions
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
0.0%
0 terminated out of 4 trials
0%
0 trials in Phase 3/4
0%
0 of 0 completed with results
Key Signals
Data Visualizations
Phase Distribution
Trial Status
Clinical Trials (4)
Observatoire Des Patients Atteints de Laminopathies et Emerinopathies (Observatory for PAtients With Laminopathies and Emerinopathies)
Modifying Factors in Striated Muscle Laminopathies
Characterization of Patients With Cardiomyopathy to Identify Critical Patients Candidates for Cardiac Transplantation
Deflazacort TREATment in LMNArelated
Research Network
Common Treatments
- Skin Biopsy1
- Deflan 2275 Mgml Gocce Orali Sospensione1
- Muscle Biopsy1
Active Sponsors
- Institut National de la Santé Et de la Recherche Médicale, France2
- IRCCS Azienda Ospedaliero-Universitaria di Bologna1
- Pitié-Salpêtrière Hospital1
- Institut de Myologie, France1
- Assistance Publique - Hôpitaux de Paris1
Top Investigators
IRCCS Azienda Ospedaliero-Universitaria
Institut National de la Santé Et de la Recherche Médicale, France
Assistance Publique - Hôpitaux de Paris
Institut de myologie
Related Conditions
- Mitochondrial Cardiomyopathy1
- Micro Rna1
- Amyloidosis Cardiac1
- Dilated Cardiomyopathy1a1
- Echocardiogram1