Condition
Lafora Disease
Total Trials
4
Recruiting
1
Active
1
Completed
2
Success Rate
100.0%+13% vs avg
Key Insights
Highlights
Success Rate
100% trial completion (above average)
Clinical Risk Assessment
Based on trial outcomes
Moderate Risk
Score: 50/100
Termination Rate
0.0%
0 terminated out of 4 trials
Success Rate
100.0%
+13.5% vs benchmark
Late-Stage Pipeline
0%
0 trials in Phase 3/4
Results Transparency
0%
0 of 2 completed with results
Key Signals
100% success
Data Visualizations
Phase Distribution
1Total
P 1 (1)
Trial Status
Completed2
Unknown1
Recruiting1
Trial Success Rate
100.0%
Benchmark: 86.5%
Based on 2 completed trials
Clinical Trials (4)
Showing 4 of 4 trials
NCT06609889Phase 1RecruitingPrimary
A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease
NCT05930223UnknownPrimary
Intravenous VAL-1221 Lafora Expanded Access Protocol
NCT03876522CompletedPrimary
Natural History and Functional Status Study of Patients With Lafora Disease
NCT00007124CompletedPrimary
Ketogenic Diet in Lafora Disease
Showing all 4 trials