Key Insights

Highlights

Research Leaders

8 sponsors active, led by Children's Hospital of Philadelphia

Clinical Risk Assessment

Based on trial outcomes

Moderate Risk

Score: 50/100

Termination Rate

0.0%

0 terminated out of 1 trials

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

0%

0 of 0 completed with results

Key Signals

Data Visualizations

Phase Distribution

Trial Status

Active Not Recruiting1

Clinical Trials (1)

Research Network

Active Sponsors

  • Children's Hospital of Philadelphia1
  • The University of Texas Health Science Center, Houston1
  • University of Iowa1
  • Columbia University1
  • National Institute of Neurological Disorders and Stroke (NINDS)1

Top Investigators

Related Conditions

  • Juvenileonset Huntington Disease1

Activity Timeline