Key Insights

Highlights

Success Rate

50% trial completion

Treatment Research

4 treatments under study, led by Cholic Acids

Related Conditions

Often studied with 5 related conditions

Clinical Risk Assessment

Based on trial outcomes

High Risk

Score: 55/100

Termination Rate

50.0%

1 terminated out of 2 trials

Success Rate

50.0%

-36.6% vs benchmark

Late-Stage Pipeline

50%

1 trials in Phase 3/4

Results Transparency

100%

1 of 1 completed with results

Key Signals

1 with results50% success

Data Visualizations

Phase Distribution

2Total
Not Applicable (1)
Phase 3 (1)

Trial Status

Terminated1
Completed1

Trial Success Rate

50.0%

Benchmark: 86.6%

Based on 1 completed trials

Clinical Trials (2)

Showing 2 of 2 trials
NCT00007020Phase 3CompletedPrimary

Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid

NCT00004442Not ApplicableTerminatedPrimary

Study of Bile Acids in Patients With Peroxisomal Disorders

Showing all 2 trials

Research Network

Common Treatments

  • Cholic Acids1
  • Ursodiol1
  • Cholic Acid1
  • Chenodeoxycholic Acid1

Active Sponsors

  • Children's Hospital Medical Center, Cincinnati2
  • University of Cincinnati1
  • Mirum Pharmaceuticals, Inc.1

Top Investigators

Related Conditions

  • Zellweger Syndrome2
  • Adrenoleukodystrophy2
  • Peroxisomal Disorders1
  • Bifunctional Enzyme Deficiency1
  • Cholestasis1

Activity Timeline